Wilson Disease: Clinical Trials

3 trials for Wilson Disease, newest first

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3 completed. 3 Phase 1.

By phase and status

PhaseTrialsStatus
Phase 13Completed 3

Follow Wilson Disease: new trials by email Literature Review of Wilson Disease trials Research Report on Wilson Disease

Trials (filtered) newest first · largest first

All 3 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Study of ALXN1840 on the Metabolism of a CYP2B6 Substrate in Healthy Participants
ALXN1840, Bupropion Hydrochloride - Wilson Disease
Phase 1CompletedAlexion Pharmaceuticals, Inc.542020-10-212023-08-31
Phase 1 Study of ALXN1840 on the Metabolism of a CYP2C9 Substrate in Healthy Participants.
ALXN1840, Celecoxib - Wilson Disease
Phase 1CompletedAlexion Pharmaceuticals, Inc.362020-07-072023-08-21
Pharmacokinetic Study of Oral ALXN1840 in Japanese and Non-Japanese Adult Healthy Participants
ALXN1840 - Wilson Disease
Phase 1CompletedAlexion Pharmaceuticals, Inc.242019-02-202023-11-07

Narrower conditions

Hepatolenticular Degeneration (3)

Broader conditions

Basal Ganglia Diseases (3)  ·  Brain Diseases (3)  ·  Brain Diseases, Metabolic (3)  ·  Brain Diseases, Metabolic, Inborn (3)  ·  Central Nervous System Diseases (3)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3)  ·  Digestive System Diseases (3)  ·  Genetic Diseases, Inborn (3)  ·  Heredodegenerative Disorders, Nervous System (3)  ·  Liver Diseases (3)  ·  Metabolic Diseases (3)  ·  Metabolism, Inborn Errors (3)  ·  Metal Metabolism, Inborn Errors (3)  ·  Movement Disorders (3)  ·  Nervous System Diseases (3)

Interventions

tetrathiomolybdate (2)  ·  Bupropion (1)  ·  Celecoxib (1)

Sponsors

Alexion Pharmaceuticals, Inc. (3)

Countries

United States (2)  ·  United Kingdom (1)

NIH funding

2018 (1)