Vitelliform Macular Dystrophy: Clinical Trials

2 trials for Vitelliform Macular Dystrophy, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

1 completed, 1 recruiting. 2 Phase 1, 2 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 12Completed 1, Recruiting 1
Phase 22Completed 1, Recruiting 1

Follow Vitelliform Macular Dystrophy: new trials by email Literature Review of Vitelliform Macular Dystrophy trials Research Report on Vitelliform Macular Dystrophy

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Safety and Tolerability of Subretinally Injected OPGx-BEST1 in Patients With Best Vitelliform Macular Dystrophy (BVMD) or Autosomal-Recessive Bestrophinopathy (ARB)
OPGx-BEST1 - ARB, BVMD
Phase 1 / Phase 2RecruitingOpus Genetics, Inc102025-09-252026-09-24
Treatment of Exudative and Vasogenic Chorioretinal Diseases Including Variants of AMD and Other CNV Related Maculopathy
ranibizumab injection (0.5 mg) - Coats' Disease, Idiopathic Retinal Telangiectasia
Phase 1 / Phase 2CompletedManhattan Eye, Ear & Throat Hospital182007-05-012012-10-25

Narrower conditions

Bestrophinopathy (1)  ·  Myopia, Degenerative (1)  ·  Polypoidal Choroidal Vasculopathy (1)  ·  Pseudoxanthoma Elasticum (1)  ·  Retinal Telangiectasis (1)  ·  von Hippel-Lindau Disease (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Eye Diseases (2)  ·  Eye Diseases, Hereditary (2)  ·  Genetic Diseases, Inborn (2)  ·  Macular Degeneration (2)  ·  Retinal Degeneration (2)  ·  Retinal Diseases (2)  ·  Abnormalities, Multiple (1)  ·  Angiomatosis (1)  ·  Cardiovascular Diseases (1)  ·  Choroid Diseases (1)  ·  Choroidal Neovascularization (1)  ·  Ciliopathies (1)  ·  Congenital Abnormalities (1)  ·  Connective Tissue Diseases (1)

Interventions

Ranibizumab (1)

Sponsors

Manhattan Eye, Ear & Throat Hospital (1)  ·  Opus Genetics, Inc (1)

Countries

United States (2)

Top investigators

Lawrence A. Yannuzzi, MD (1)