Thalassemia, Beta: Clinical Trials

9 trials for Thalassemia, Beta, newest first

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4 recruiting, 3 completed, 1 terminated, 1 unknown. 4 Phase 2, 2 Not applicable, 2 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 24Completed 2, Recruiting 1, Unknown 1
Not applicable2Completed 1, Terminated 1
Phase 32Completed 2

Follow Thalassemia, Beta: new trials by email Literature Review of Thalassemia, Beta trials Research Report on Thalassemia, Beta

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Long-term Follow-up Study of BRL-101 for TDT
Assessments - Thalassemia, Beta
RecruitingBioray Laboratories452024-12-082026-07-21
Impact of Virtual Reality on Pain and Anxiety During Intravenous Cannulation Procedures Among Thalassemia Patients in UAE.
Headset-based Virtual Reality Simulation - Thalassemia, Beta, Thalassemia
Not applicableCompletedMohammed Bin Rashid University of Medicine and Health Sciences1152024-05-242025-08-01
Safety and Efficacy Evaluation of Autologous CRISPR-Cas12b Edited Hematopoietic Stem Cells
VGB-Ex01 - Thalassemia, Beta, Thalassemia Major
Not applicableTerminatedInstitute of Hematology & Blood Diseases Hospital, China12023-08-312026-11-04
A Study of Immune Suppression Treatment for People With Sickle Cell Disease or β-Thalassemia Who Are Going to Receive an Allogeneic Hematopoietic Cell Transplantation (HCT)
Fludarabine, Cyclophosphamide, Tacrolimus - Sickle Cell Disease, Thalassemia, Beta
Phase 2RecruitingMemorial Sloan Kettering Cancer Center242023-02-092026-06-03
Long-term Follow-up Study of BHC001 for TDT
Assessments - Thalassemia, Beta
RecruitingBioray Laboratories62022-12-142024-03-18
Study of the Role of Genetic Modifiers in Hemoglobinopathies
GWAS - Sickle Cell Disease, Thalassemia, Beta
RecruitingCyprus Institute of Neurology and Genetics300002022-10-012024-03-20
Thalidomide and Hydroxyurea Combination in β-Thalassemia Patients
Hydroxyurea and Thalidomide - Thalassemia, Beta
Phase 2 / Phase 3CompletedChildren's Hospital Karachi6032020-07-072023-12-01
Clinical Experience of Thalidomide in Thalassemic Patients
hydroxyurea and thalidomide - Thalassemia, Beta
Phase 2 / Phase 3CompletedChildren's Hospital Karachi1352020-01-012021-11-24
The Efficacy and Safety of HYDROXYUREA in Management of Beta Thalassemia Patients in Karachi Pakistan
Hydroxyurea - Thalassemia, Beta
Phase 2UnknownDr.Saqib Hussain Ansari1002017-08-212017-09-20

Narrower conditions

beta-Thalassemia (9)  ·  Thalassemia (3)  ·  Anemia, Sickle Cell (2)  ·  Anxiety Disorders (1)  ·  Hematologic Diseases (1)  ·  Hemoglobinopathies (1)  ·  Pain (1)  ·  alpha-Thalassemia (1)

Broader conditions

Anemia (9)  ·  Anemia, Hemolytic (9)  ·  Anemia, Hemolytic, Congenital (9)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (9)  ·  Genetic Diseases, Inborn (9)  ·  Hemic and Lymphatic Diseases (9)  ·  Hematologic Diseases (8)  ·  Hemoglobinopathies (8)  ·  Thalassemia (6)  ·  Mental Disorders (1)  ·  Neurologic Manifestations (1)  ·  Pathological Conditions, Signs and Symptoms (1)  ·  Signs and Symptoms (1)

Interventions

Hydroxyurea (3)  ·  Thalidomide (2)  ·  Bortezomib (1)  ·  Cyclophosphamide (1)  ·  Dexamethasone (1)  ·  Mycophenolic Acid (1)  ·  Rituximab (1)  ·  Tacrolimus (1)  ·  fludarabine (1)  ·  thymoglobulin (1)

Sponsors

Bioray Laboratories (2)  ·  Children's Hospital Karachi (2)  ·  Cyprus Institute of Neurology and Genetics (1)  ·  Dr.Saqib Hussain Ansari (1)  ·  Institute of Hematology & Blood Diseases Hospital, China (1)  ·  Memorial Sloan Kettering Cancer Center (1)  ·  Mohammed Bin Rashid University of Medicine and Health Sciences (1)

Countries

Pakistan (4)  ·  China (3)  ·  United States (2)  ·  Angola (1)  ·  Argentina (1)  ·  Belgium (1)  ·  Brunei (1)  ·  Cyprus (1)  ·  Democratic Republic of the Congo (1)  ·  Denmark (1)  ·  Greece (1)  ·  Israel (1)  ·  Italy (1)  ·  Malaysia (1)  ·  Nigeria (1)

Top investigators

Jun Shi, PhD (1)  ·  Maria Cancio, MD (1)  ·  Petros Kountouris, PhD (1)  ·  Rongmei Liang, PhD (1)  ·  Saqib H Ansari, MBBS, DCH, DPGN, Mphil, PhD (1)  ·  Saqib H Ansari, Phd (1)  ·  Xiaochen Wang, PhD (1)

Results publications

PMID 35477175