2 completed, 1 recruiting, 1 unknown. 4 Phase 2, 2 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 4 | Completed 2, Recruiting 1, Unknown 1 |
| Phase 3 | 2 | Completed 2 |
Follow Thalassemia, Beta: new trials by email Literature Review of Thalassemia, Beta trials Research Report on Thalassemia, Beta
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Study of Immune Suppression Treatment for People With Sickle Cell Disease or β-Thalassemia Who Are Going to Receive an Allogeneic Hematopoietic Cell Transplantation (HCT) Fludarabine, Cyclophosphamide, Tacrolimus - Sickle Cell Disease, Thalassemia, Beta | Phase 2 | Recruiting | Memorial Sloan Kettering Cancer Center | 24 | 2023-02-09 | 2026-06-03 |
| Thalidomide and Hydroxyurea Combination in β-Thalassemia Patients Hydroxyurea and Thalidomide - Thalassemia, Beta | Phase 2 / Phase 3 | Completed | Children's Hospital Karachi | 603 | 2020-07-07 | 2023-12-01 |
| Clinical Experience of Thalidomide in Thalassemic Patients hydroxyurea and thalidomide - Thalassemia, Beta | Phase 2 / Phase 3 | Completed | Children's Hospital Karachi | 135 | 2020-01-01 | 2021-11-24 |
| The Efficacy and Safety of HYDROXYUREA in Management of Beta Thalassemia Patients in Karachi Pakistan Hydroxyurea - Thalassemia, Beta | Phase 2 | Unknown | Dr.Saqib Hussain Ansari | 100 | 2017-08-21 | 2017-09-20 |
beta-Thalassemia (4) · Anemia, Sickle Cell (1) · Thalassemia (1)
Anemia (4) · Anemia, Hemolytic (4) · Anemia, Hemolytic, Congenital (4) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (4) · Genetic Diseases, Inborn (4) · Hematologic Diseases (4) · Hemic and Lymphatic Diseases (4) · Hemoglobinopathies (4) · Thalassemia (3)
Hydroxyurea (3) · Thalidomide (2) · Bortezomib (1) · Cyclophosphamide (1) · Dexamethasone (1) · Mycophenolic Acid (1) · Rituximab (1) · Tacrolimus (1) · fludarabine (1) · thymoglobulin (1)
Children's Hospital Karachi (2) · Dr.Saqib Hussain Ansari (1) · Memorial Sloan Kettering Cancer Center (1)
Pakistan (3) · United States (1)
Maria Cancio, MD (1) · Saqib H Ansari, MBBS, DCH, DPGN, Mphil, PhD (1) · Saqib H Ansari, Phd (1)