1 recruiting. 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 3 | 1 | Recruiting 1 |
Follow Septo-Optic Dysplasia: new trials by email Literature Review of Septo-Optic Dysplasia trials Research Report on Septo-Optic Dysplasia
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Trial of Setmelanotide in Patients With Congenital Hypothalamic Obesity (Sub-study of NCT05774756) Setmelanotide, Placebo - Hypothalamic Obesity, Multiple Pituitary Hormone Deficiency Genetic Form | Phase 3 | Recruiting | Rhythm Pharmaceuticals, Inc. | 39 | 2025-09-23 | 2026-02-12 |
Optic Nerve Hypoplasia (1) · Sexual Infantilism (1)
Agenesis of Corpus Callosum (1) · Congenital Abnormalities (1) · Congenital Cranial Dysinnervation Disorders (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Cranial Nerve Diseases (1) · Disorders of Sex Development (1) · Endocrine System Diseases (1) · Eye Diseases (1) · Eye Diseases, Hereditary (1) · Female Urogenital Diseases (1) · Female Urogenital Diseases and Pregnancy Complications (1) · Genetic Diseases, Inborn (1) · Gonadal Disorders (1) · Gonadal Dysgenesis (1) · Hypogonadism (1)
setmelanotide (1)
Rhythm Pharmaceuticals, Inc. (1)
United Kingdom (1) · United States (1)
David Meeker, MD (1)