Septo-Optic Dysplasia: Clinical Trials

1 trial for Septo-Optic Dysplasia, newest first

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1 recruiting. 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 31Recruiting 1

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Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Trial of Setmelanotide in Patients With Congenital Hypothalamic Obesity (Sub-study of NCT05774756)
Setmelanotide, Placebo - Hypothalamic Obesity, Multiple Pituitary Hormone Deficiency Genetic Form
Phase 3RecruitingRhythm Pharmaceuticals, Inc.392025-09-232026-02-12

Narrower conditions

Optic Nerve Hypoplasia (1)  ·  Sexual Infantilism (1)

Broader conditions

Agenesis of Corpus Callosum (1)  ·  Congenital Abnormalities (1)  ·  Congenital Cranial Dysinnervation Disorders (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Cranial Nerve Diseases (1)  ·  Disorders of Sex Development (1)  ·  Endocrine System Diseases (1)  ·  Eye Diseases (1)  ·  Eye Diseases, Hereditary (1)  ·  Female Urogenital Diseases (1)  ·  Female Urogenital Diseases and Pregnancy Complications (1)  ·  Genetic Diseases, Inborn (1)  ·  Gonadal Disorders (1)  ·  Gonadal Dysgenesis (1)  ·  Hypogonadism (1)

Interventions

setmelanotide (1)

Sponsors

Rhythm Pharmaceuticals, Inc. (1)

Countries

United Kingdom (1)  ·  United States (1)

Top investigators

David Meeker, MD (1)