2 completed. 2 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 2 | Completed 2 |
Follow Propionic Acidemia: new trials by email Literature Review of Propionic Acidemia trials Research Report on Propionic Acidemia
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Short-Term Outcome of N-Carbamylglutamate in the Treatment of Acute Hyperammonemia Carbaglu, Placebo - Propionic Acidemia, Type I and/or Type II, Methylmalonic Acidemia | Phase 2 | Completed | Mendel Tuchman | 35 | 2012-09-01 | 2021-02-15 |
| Pilot Study For Hypothermia Treatment In Hyperammonemic Encephalopathy In Neonates And Very Young Infants Therapeutic Hypothermia, Standard of Care Therapy - Urea Cycle Disorders, Organic Acidemias | Phase 2 | Completed | Uta Lichter-Konecki | 5 | 2007-08-01 | 2015-06-01 |
Carbamoyl-Phosphate Synthase I Deficiency Disease (2) · Hyperammonemia (2) · Methylmalonic acidemia (2) · Ornithine Carbamoyltransferase Deficiency Disease (2) · Argininosuccinic Aciduria (1) · Brain Diseases (1) · Brain Edema (1) · Citrullinemia (1) · Coma (1) · Lethargy (1) · Seizures (1) · Urea Cycle Disorders, Inborn (1)
Amino Acid Metabolism, Inborn Errors (2) · Brain Diseases, Metabolic (2) · Brain Diseases, Metabolic, Inborn (2) · Central Nervous System Diseases (2) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Genetic Diseases, Inborn (2) · Genetic Diseases, X-Linked (2) · Metabolic Diseases (2) · Metabolism, Inborn Errors (2) · Mitochondrial Diseases (2) · Nervous System Diseases (2) · Nutritional and Metabolic Diseases (2) · Pathologic Processes (2) · Pathological Conditions, Signs and Symptoms (2) · Brain Diseases (1)
Continuous Renal Replacement Therapy (1) · Cool-Down Exercise (1) · Cryotherapy (1) · Dialysis (1) · Hypothermia, Induced (1) · Renal Dialysis (1) · carglumic acid (1)
Mendel Tuchman (1) · Uta Lichter-Konecki (1)
United States (2)
Mendel Tuchman, MD (1) · Uta Lichter-Konecki, MD, PhD (1)