1 completed, 1 unknown. .
Follow Peroneal Muscular Atrophy: new trials by email Literature Review of Peroneal Muscular Atrophy trials Research Report on Peroneal Muscular Atrophy
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Genetics of Charcot-Marie-Tooth Dystrophy and Related Diseases basic information, venous blood test - Peroneal Muscular Atrophy | Unknown | Peking University Third Hospital | 200 | 2018-11-01 | 2021-07-19 | |
| Genetics of Pediatric-Onset Motor Neuron and Neuromuscular Diseases sample collection - Spinal Muscular Atrophy, Charcot-Marie-Tooth Disease | Completed | Nemours Children's Clinic | 230 | 2015-06-01 | 2024-12-19 |
Charcot-Marie-Tooth Disease (2) · Amyotrophic Lateral Sclerosis (1) · Motor Neuron Disease (1) · Muscular Atrophy, Spinal (1) · Muscular Dystrophies (1) · Neuromuscular Diseases (1) · Spinal muscular atrophy with respiratory distress 1 (1)
Congenital Abnormalities (2) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Genetic Diseases, Inborn (2) · Hereditary Sensory and Motor Neuropathy (2) · Heredodegenerative Disorders, Nervous System (2) · Nervous System Diseases (2) · Nervous System Malformations (2) · Neurodegenerative Diseases (2) · Peripheral Nervous System Diseases (2) · Polyneuropathies (2) · Central Nervous System Diseases (1) · Metabolic Diseases (1) · Muscular Diseases (1) · Muscular Disorders, Atrophic (1) · Musculoskeletal Diseases (1)
Nemours Children's Clinic (1) · Peking University Third Hospital (1)
China (1) · United States (1)
Matthew ER Butchbach, Ph.D. (1) · Xiaoxuan Liu (1)
PMID 26247043, PMID 28284873, PMID 32066871, PMID 33199817, PMID 33415588, PMID 35741345