Peroneal Muscular Atrophy: Clinical Trials

2 trials for Peroneal Muscular Atrophy, newest first

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1 completed, 1 unknown. .

Follow Peroneal Muscular Atrophy: new trials by email Literature Review of Peroneal Muscular Atrophy trials Research Report on Peroneal Muscular Atrophy

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Genetics of Charcot-Marie-Tooth Dystrophy and Related Diseases
basic information, venous blood test - Peroneal Muscular Atrophy
UnknownPeking University Third Hospital2002018-11-012021-07-19
Genetics of Pediatric-Onset Motor Neuron and Neuromuscular Diseases
sample collection - Spinal Muscular Atrophy, Charcot-Marie-Tooth Disease
CompletedNemours Children's Clinic2302015-06-012024-12-19

Narrower conditions

Charcot-Marie-Tooth Disease (2)  ·  Amyotrophic Lateral Sclerosis (1)  ·  Motor Neuron Disease (1)  ·  Muscular Atrophy, Spinal (1)  ·  Muscular Dystrophies (1)  ·  Neuromuscular Diseases (1)  ·  Spinal muscular atrophy with respiratory distress 1 (1)

Broader conditions

Congenital Abnormalities (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Genetic Diseases, Inborn (2)  ·  Hereditary Sensory and Motor Neuropathy (2)  ·  Heredodegenerative Disorders, Nervous System (2)  ·  Nervous System Diseases (2)  ·  Nervous System Malformations (2)  ·  Neurodegenerative Diseases (2)  ·  Peripheral Nervous System Diseases (2)  ·  Polyneuropathies (2)  ·  Central Nervous System Diseases (1)  ·  Metabolic Diseases (1)  ·  Muscular Diseases (1)  ·  Muscular Disorders, Atrophic (1)  ·  Musculoskeletal Diseases (1)

Interventions

Specimen Handling (1)

Sponsors

Nemours Children's Clinic (1)  ·  Peking University Third Hospital (1)

Countries

China (1)  ·  United States (1)

Top investigators

Matthew ER Butchbach, Ph.D. (1)  ·  Xiaoxuan Liu (1)

Results publications

PMID 26247043, PMID 28284873, PMID 32066871, PMID 33199817, PMID 33415588, PMID 35741345