1 completed. 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Completed 1 |
| Phase 2 | 1 | Completed 1 |
Follow Occipital horn syndrome: new trials by email Literature Review of Occipital horn syndrome trials Research Report on Occipital horn syndrome
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| NORTHERA (DROXIDOPA) for Dysautonomia in Adult Survivors of Menkes Disease and Occipital Horn Syndrome Droxidopa, Placebo - Menkes Disease, Occipital Horn Syndrome | Phase 1 / Phase 2 | Completed | Stephen G. Kaler, MD | 3 | 2021-07-12 | 2026-04-13 |
Autonomic Nervous System Diseases (1) · Menkes Kinky Hair Syndrome (1)
Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Central Nervous System Diseases (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Genetic Diseases, X-Linked (1) · Hair Diseases (1) · Heredodegenerative Disorders, Nervous System (1) · Intellectual Disability (1) · Metabolic Diseases (1) · Metabolism, Inborn Errors (1) · Metal Metabolism, Inborn Errors (1) · Nervous System Diseases (1) · Neurobehavioral Manifestations (1)
Droxidopa (1)
United States (1)