2 completed. 1 Phase 1, 1 Phase 2, 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Completed 1 |
| Phase 2 | 1 | Completed 1 |
| Phase 3 | 1 | Completed 1 |
Follow Occipital horn syndrome: new trials by email Literature Review of Occipital horn syndrome trials Research Report on Occipital horn syndrome
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| NORTHERA (DROXIDOPA) for Dysautonomia in Adult Survivors of Menkes Disease and Occipital Horn Syndrome Droxidopa, Placebo - Menkes Disease, Occipital Horn Syndrome | Phase 1 / Phase 2 | Completed | Stephen G. Kaler, MD | 3 | 2021-07-12 | 2026-04-13 |
| Molecular Bases of Response to Copper Treatment in Menkes Disease, Related Phenotypes, and Unexplained Copper Deficiency Copper Histidine - Menkes Disease, Occipital Horn Syndrome | Phase 3 | Completed | Cyprium Therapeutics, Inc. | 93 | 2009-02-27 | 2020-11-19 |
Menkes Kinky Hair Syndrome (2) · Autonomic Nervous System Diseases (1) · Nerve Degeneration (1)
Brain Diseases (2) · Brain Diseases, Metabolic (2) · Brain Diseases, Metabolic, Inborn (2) · Central Nervous System Diseases (2) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Genetic Diseases, Inborn (2) · Genetic Diseases, X-Linked (2) · Hair Diseases (2) · Heredodegenerative Disorders, Nervous System (2) · Intellectual Disability (2) · Metabolic Diseases (2) · Metabolism, Inborn Errors (2) · Metal Metabolism, Inborn Errors (2) · Nervous System Diseases (2) · Neurobehavioral Manifestations (2)
Droxidopa (1) · copper histidine (1)
Cyprium Therapeutics, Inc. (1) · Stephen G. Kaler, MD (1)
United States (2)