1 recruiting, 1 unknown. 2 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 3 | 2 | Recruiting 1, Unknown 1 |
Follow Neonatal Disease: new trials by email Literature Review of Neonatal Disease trials Research Report on Neonatal Disease
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Phase 3 Study to Evaluate the Safety and Efficacy of AOC 1044 (Also Referred to as Delpacibart Zotadirsen) in Participants With DMD With Gene Mutations Amenable to Exon 44 Skipping AOC 1044, Placebo - Muscular Dystrophies, Muscular Dystrophies (Duchenne, Becker, Myotonic Dystrophy) | Phase 3 | Recruiting | Avidity Biosciences, Inc. | 70 | 2026-09-01 | 2026-10-13 |
| Prevention of Metabolic Acidosis in Preterm Neonates by Replacing Sodium Chloride With Sodium Acetate in Parenteral Nutrition sodium acetate group will receive sodium acetate in the neonatal PN., sodium chloride group will receive sodium chloride in the neonatal PN. - Metabolic Acidosis, Neonatal Disease | Phase 3 | Unknown | Aga Khan University Hospital, Pakistan | 200 | 2024-07-10 | 2024-08-09 |
Infant, Newborn, Diseases (2) · Acidosis (1) · Genetic Diseases, Inborn (1) · Hyperphagia (1) · Muscular Diseases (1) · Muscular Disorders, Atrophic (1) · Muscular Dystrophies (1) · Muscular Dystrophy, Duchenne (1) · Musculoskeletal Diseases (1) · Myotonic Dystrophy (1) · Nervous System Diseases (1) · Neuromuscular Diseases (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Acid-Base Imbalance (1) · Genetic Diseases, X-Linked (1) · Heredodegenerative Disorders, Nervous System (1) · Metabolic Diseases (1) · Myotonic Disorders (1) · Neurodegenerative Diseases (1) · Nutritional and Metabolic Diseases (1) · Pathological Conditions, Signs and Symptoms (1) · Signs and Symptoms (1) · Signs and Symptoms, Digestive (1)
Sodium Acetate (1) · Sodium Chloride (1)
Aga Khan University Hospital, Pakistan (1) · Avidity Biosciences, Inc. (1)
Australia (1) · Belgium (1) · France (1) · Germany (1) · Italy (1) · Netherlands (1) · Pakistan (1) · Spain (1) · United Kingdom (1)