Mitochondrial Disorders: Clinical Trials

10 trials for Mitochondrial Disorders, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

6 completed, 3 recruiting, 1 enrolling by invitation. 3 Not applicable.

By phase and status

PhaseTrialsStatus
Not applicable3Completed 3

Follow Mitochondrial Disorders: new trials by email Literature Review of Mitochondrial Disorders trials Research Report on Mitochondrial Disorders

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Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Exercise-mediated Rescue of Mitochondrial Dysfunctions Driving Insulin Resistance
High-intensity exercise training - Mitochondrial Myopathies, Mitochondrial Diseases
Not applicableCompletedCopenhagen University Hospital, Rigshospitalet112024-09-222025-06-22
Mitochondrial Disease-associated ImmunoDeficiencies
Patient cohort, Control cohort - Mitochondrial Disorders
RecruitingUniversity Hospital, Bordeaux602024-01-302026-02-03
Mitochondrial Dysfunctions Driving Insulin Resistance
Mitochondrial Myopathies, Mitochondrial Diseases
CompletedCopenhagen University Hospital, Rigshospitalet302023-10-202025-06-22
Mitochondrial Cocktail for Gulf War Illness
Individualized mitochondrial cocktail, Placebo - Gulf War Syndrome, Persian Gulf Syndrome
Not applicableCompletedUniversity of California, San Diego152021-04-092023-04-05
DINAMITE Study Nutritional State and Effect Diet in Mitochondrial Disease
diet intervention - Mitochondrial Disorders
Not applicableCompletedRadboud University Medical Center402014-03-012017-04-14
The NIH MINI Study: Metabolism, Infection, and Immunity in Inborn Errors of Metabolism
Oxidative Phosphorylation Deficiencies, Electron Transport Chain Disorders, Mitochondrial
RecruitingNational Human Genome Research Institute (NHGRI)5002012-12-312026-10-28
Tissue Sample Study for Mitochondrial Disorders
Mitochondrial Disorders, Mitochondrial Disease
Enrolling by invitationColumbia University69002012-02-012026-01-07
North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)
Mitochondrial Disorders, Mitochondrial Genetic Disorders
RecruitingColumbia University10002011-01-312026-02-04
Gastrointestinal Dysfunction in Children Affected With Mitochondrial Disorders
gastric emptying scan - Gastrointestinal Dysfunction, Mitochondrial Disorders
CompletedThe University of Texas Health Science Center, Houston262010-06-012012-02-27
Role of p53 Gene in Metabolism Regulation in Patients With Li-Fraumeni Syndrome
Mitochondrial Disorders, Li-Fraumeni Syndrome
CompletedNational Heart, Lung, and Blood Institute (NHLBI)822007-01-232021-11-22

Narrower conditions

Mitochondrial Diseases (10)  ·  Leigh Disease (3)  ·  Mitochondrial Myopathies (3)  ·  Insulin Resistance (2)  ·  MELAS Syndrome (2)  ·  Acidosis, Lactic (1)  ·  Barth Syndrome (1)  ·  Brain Diseases (1)  ·  Cytochrome-c Oxidase Deficiency (1)  ·  Deafness (1)  ·  Diabetes Mellitus (1)  ·  Kearns-Sayre Syndrome (1)  ·  Leukoencephalopathies (1)  ·  Li-Fraumeni Syndrome (1)  ·  MERRF Syndrome (1)

Broader conditions

Metabolic Diseases (10)  ·  Nutritional and Metabolic Diseases (10)  ·  Nervous System Diseases (5)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (4)  ·  Genetic Diseases, Inborn (4)  ·  Muscular Diseases (4)  ·  Musculoskeletal Diseases (4)  ·  Neuromuscular Diseases (4)  ·  Brain Diseases, Metabolic (3)  ·  Brain Diseases, Metabolic, Inborn (3)  ·  Carbohydrate Metabolism, Inborn Errors (3)  ·  Central Nervous System Diseases (3)  ·  Glucose Metabolism Disorders (3)  ·  Metabolism, Inborn Errors (3)  ·  Pyruvate Metabolism, Inborn Errors (3)

Interventions

High-Intensity Interval Training (1)

Sponsors

Columbia University (2)  ·  Copenhagen University Hospital, Rigshospitalet (2)  ·  National Heart, Lung, and Blood Institute (NHLBI) (1)  ·  National Human Genome Research Institute (NHGRI) (1)  ·  Radboud University Medical Center (1)  ·  The University of Texas Health Science Center, Houston (1)  ·  University Hospital, Bordeaux (1)  ·  University of California, San Diego (1)

Countries

United States (6)  ·  Denmark (2)  ·  Canada (1)  ·  France (1)

Top investigators

John Vissing, MD (2)  ·  Matteo Fiorenza, Ph.D. (2)  ·  Michio Hirano, MD (2)  ·  Jatinder Bhardwaj, MD (1)  ·  Mary K Koenig, MD (1)  ·  Paul M Hwang, M.D. (1)  ·  Peter J McGuire, M.D. (1)

Results publications

PMID 23484829, PMID 27869650

NIH funding

P01HD032062 (1), U54NS078059 (1)