2 recruiting. .
Follow Maternally Inherited Leigh Syndrome: new trials by email Literature Review of Maternally Inherited Leigh Syndrome trials Research Report on Maternally Inherited Leigh Syndrome
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC) Mitochondrial Disorders, Mitochondrial Genetic Disorders | Recruiting | Columbia University | 1000 | 2011-01-31 | 2026-02-04 | |
| Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford Rare Disorders, Undiagnosed Disorders | Recruiting | Sanford Health | 20000 | 2010-07-01 | 2026-10-28 |
Deafness (2) · Leigh Disease (2) · Mitochondrial Diseases (2) · Neuropathy ataxia and retinitis pigmentosa (2) · Syndrome (2) · 3-Methylglutaconic Aciduria, Type V (1) · Achalasia Addisonianism Alacrimia syndrome (1) · Acidosis, Lactic (1) · Acrodysostosis (1) · Activated PI3K-delta Syndrome (1) · Addison Disease (1) · Alagille Syndrome (1) · Alstrom Syndrome (1) · Amnesia, Transient Global (1)
Abnormalities, Multiple (2) · Brain Diseases, Metabolic (2) · Brain Diseases, Metabolic, Inborn (2) · Carbohydrate Metabolism, Inborn Errors (2) · Cardiovascular Abnormalities (2) · Cardiovascular Diseases (2) · Central Nervous System Diseases (2) · Cerebrovascular Disorders (2) · Chronic Disease (2) · Congenital Abnormalities (2) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Cranial Nerve Diseases (2) · Disease (2) · Disease Attributes (2) · Ear Diseases (2)
Columbia University (1) · Sanford Health (1)
United States (2) · Canada (1)
U54NS078059 (1)