2 completed. 2 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 2 | Completed 2 |
| Phase 2 | 1 | Completed 1 |
Follow Glycogen Storage Disease Id: new trials by email Literature Review of Glycogen Storage Disease Id trials Research Report on Glycogen Storage Disease Id
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Study of Mavorixafor in Participants With Congenital Neutropenia and Chronic Idiopathic Neutropenia Disorders Mavorixafor - Neutropenia | Phase 1 / Phase 2 | Completed | X4 Pharmaceuticals | 32 | 2021-10-16 | 2025-08-06 |
| Treatment Development of Triheptanoin (G1D) Triheptanoin - Epilepsy, GLUT1DS1 | Phase 1 | Completed | Juan Pascual | 12 | 2017-03-29 | 2022-12-22 |
Epilepsy (1) · Glucose Metabolism Disorders (1) · Glut1 Deficiency Syndrome (1) · Neutropenia (1)
Agranulocytosis (1) · Brain Diseases (1) · Central Nervous System Diseases (1) · Cytopenia (1) · Hematologic Diseases (1) · Hemic and Lymphatic Diseases (1) · Leukocyte Disorders (1) · Leukopenia (1) · Metabolic Diseases (1) · Nervous System Diseases (1) · Nutritional and Metabolic Diseases (1)
mavorixafor (1) · triheptanoin (1)
Juan Pascual (1) · X4 Pharmaceuticals (1)
United States (2)
Juan Pascual (1)
R01NS094257 (1)