Glycogen Storage Disease Id: Clinical Trials

4 trials for Glycogen Storage Disease Id, newest first

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3 completed, 1 recruiting. 2 Phase 1, 2 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 12Completed 2
Phase 22Completed 2

Follow Glycogen Storage Disease Id: new trials by email Literature Review of Glycogen Storage Disease Id trials Research Report on Glycogen Storage Disease Id

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Brain Metabolism Observed at 3 Tesla or 7 Tesla in Health and Metabolic Disease
Magnetic resonance imaging - Glut1 Deficiency Syndrome 1, Glucose Metabolism Disorders
RecruitingWeill Medical College of Cornell University202022-05-032026-06-01
A Study of Mavorixafor in Participants With Congenital Neutropenia and Chronic Idiopathic Neutropenia Disorders
Mavorixafor - Neutropenia
Phase 1 / Phase 2CompletedX4 Pharmaceuticals322021-10-162025-08-06
Diet Treatment Glucose Transporter Type 1 Deficiency (G1D)
Triheptanoin - GLUT1DS1, Epilepsy
Phase 2CompletedUniversity of Texas Southwestern Medical Center452018-04-182025-08-07
Treatment Development of Triheptanoin (G1D)
Triheptanoin - Epilepsy, GLUT1DS1
Phase 1CompletedJuan Pascual122017-03-292022-12-22

Narrower conditions

Epilepsy (3)  ·  Glucose Metabolism Disorders (3)  ·  Glut1 Deficiency Syndrome (3)  ·  Neutropenia (1)

Broader conditions

Brain Diseases (3)  ·  Central Nervous System Diseases (3)  ·  Metabolic Diseases (3)  ·  Nervous System Diseases (3)  ·  Nutritional and Metabolic Diseases (3)  ·  Agranulocytosis (1)  ·  Cytopenia (1)  ·  Hematologic Diseases (1)  ·  Hemic and Lymphatic Diseases (1)  ·  Leukocyte Disorders (1)  ·  Leukopenia (1)

Interventions

triheptanoin (2)  ·  Magnetic Resonance Imaging (1)  ·  mavorixafor (1)

Sponsors

Juan Pascual (1)  ·  University of Texas Southwestern Medical Center (1)  ·  Weill Medical College of Cornell University (1)  ·  X4 Pharmaceuticals (1)

Countries

United States (4)

Top investigators

Juan Pascual (1)  ·  Juan Pascual, MD (1)

Results publications

PMID 36859467

NIH funding

R01NS094257 (2), RM1NS133593 (1)