Friedreich Ataxia: Clinical Trials

2 trials for Friedreich Ataxia, newest first

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2 completed. 2 Early Phase 1.

By phase and status

PhaseTrialsStatus
Early Phase 12Completed 2

Follow Friedreich Ataxia: new trials by email Literature Review of Friedreich Ataxia trials Research Report on Friedreich Ataxia

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Rosuvastatin (Crestor) in Friedreich Ataxia
Rosuvastatin - Friedreich Ataxia
Early Phase 1CompletedChildren's Hospital of Philadelphia122016-05-012021-03-25
Methylprednisolone Treatment of Friedreich Ataxia
Methylprednisolone - Friedreich Ataxia
Early Phase 1CompletedChildren's Hospital of Philadelphia112015-06-012021-03-25

Broader conditions

Brain Diseases (2)  ·  Central Nervous System Diseases (2)  ·  Cerebellar Diseases (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Genetic Diseases, Inborn (2)  ·  Heredodegenerative Disorders, Nervous System (2)  ·  Metabolic Diseases (2)  ·  Mitochondrial Diseases (2)  ·  Nervous System Diseases (2)  ·  Neurodegenerative Diseases (2)  ·  Nutritional and Metabolic Diseases (2)  ·  Spinal Cord Diseases (2)  ·  Spinocerebellar Degenerations (2)

Interventions

Methylprednisolone (1)  ·  Rosuvastatin Calcium (1)

Sponsors

Children's Hospital of Philadelphia (2)

Countries

United States (2)

Top investigators

David Lynch, MD PhD (1)  ·  David R Lynch, MD PhD (1)