2 completed. 2 Early Phase 1.
| Phase | Trials | Status |
|---|---|---|
| Early Phase 1 | 2 | Completed 2 |
Follow Friedreich Ataxia: new trials by email Literature Review of Friedreich Ataxia trials Research Report on Friedreich Ataxia
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Rosuvastatin (Crestor) in Friedreich Ataxia Rosuvastatin - Friedreich Ataxia | Early Phase 1 | Completed | Children's Hospital of Philadelphia | 12 | 2016-05-01 | 2021-03-25 |
| Methylprednisolone Treatment of Friedreich Ataxia Methylprednisolone - Friedreich Ataxia | Early Phase 1 | Completed | Children's Hospital of Philadelphia | 11 | 2015-06-01 | 2021-03-25 |
Brain Diseases (2) · Central Nervous System Diseases (2) · Cerebellar Diseases (2) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Genetic Diseases, Inborn (2) · Heredodegenerative Disorders, Nervous System (2) · Metabolic Diseases (2) · Mitochondrial Diseases (2) · Nervous System Diseases (2) · Neurodegenerative Diseases (2) · Nutritional and Metabolic Diseases (2) · Spinal Cord Diseases (2) · Spinocerebellar Degenerations (2)
Methylprednisolone (1) · Rosuvastatin Calcium (1)
Children's Hospital of Philadelphia (2)
United States (2)
David Lynch, MD PhD (1) · David R Lynch, MD PhD (1)