Down Syndrome: Clinical Trials

3 trials for Down Syndrome, newest first

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3 withdrawn. 3 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 23Withdrawn 3

Follow Down Syndrome: new trials by email Literature Review of Down Syndrome trials Research Report on Down Syndrome

Trials (filtered) newest first · largest first

All 3 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Trial to Evaluate Safety and Efficacy of GM-CSF /Sargramostim in Down Syndrome
Sargramostim for Injection, Saline Placebo - Down Syndrome
Phase 2WithdrawnUniversity of Colorado, Denver2023-10-232025-04-02
A Study of ACI-24 in Adults With Down Syndrome
ACI-24, Placebo - Down Syndrome
Phase 2WithdrawnAC Immune SA2021-10-012021-10-22
Liq-NOL Efficacy in Pediatric Patients With Down Syndrome
Ubiquinol-10 Syrup, syrup (placebo) - Down Syndrome
Phase 2WithdrawnChildren's Hospital Medical Center, Cincinnati2005-01-012020-09-09

Narrower conditions

Behavior (1)  ·  Cognitive Dysfunction (1)  ·  Language (1)

Broader conditions

Abnormalities, Multiple (3)  ·  Chromosome Disorders (3)  ·  Congenital Abnormalities (3)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3)  ·  Genetic Diseases, Inborn (3)  ·  Intellectual Disability (3)  ·  Nervous System Diseases (3)  ·  Neurobehavioral Manifestations (3)  ·  Neurologic Manifestations (3)  ·  Cognition Disorders (1)  ·  Communication (1)  ·  Mental Disorders (1)  ·  Neurocognitive Disorders (1)

Interventions

Granulocyte-Macrophage Colony-Stimulating Factor (1)  ·  Injections (1)  ·  sargramostim (1)

Sponsors

AC Immune SA (1)  ·  Children's Hospital Medical Center, Cincinnati (1)  ·  University of Colorado, Denver (1)

Countries

United States (2)

Top investigators

Francis Hickey, M.D. (1)  ·  Michael S. Rafii, MD, PhD (1)  ·  Michael V Miles, Pharm.D. (1)  ·  Peter Pressman, MD (1)

Results publications

PMID 33778150, PMID 35307513

NIH funding

R61AG074859 (1)