1 withdrawn. 1 Phase 1.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Withdrawn 1 |
Follow Cardiomyopathy: new trials by email Literature Review of Cardiomyopathy trials Research Report on Cardiomyopathy
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Study of ASP2016 in Adults Who Have Heart Disease Associated With Friedreich Ataxia ASP2016, Prednisolone - Friedreich Ataxia, Cardiomyopathy | Phase 1 | Withdrawn | Astellas Gene Therapies | 2024-11-08 | 2025-11-28 |
Cardiomyopathies (1) · Friedreich Ataxia (1)
Brain Diseases (1) · Cardiovascular Diseases (1) · Central Nervous System Diseases (1) · Cerebellar Diseases (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Heart Diseases (1) · Heredodegenerative Disorders, Nervous System (1) · Metabolic Diseases (1) · Mitochondrial Diseases (1) · Nervous System Diseases (1) · Neurodegenerative Diseases (1) · Nutritional and Metabolic Diseases (1) · Spinal Cord Diseases (1) · Spinocerebellar Degenerations (1)
Prednisolone (1)