4 active not recruiting. 4 Phase 3, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 3 | 4 | Active not recruiting 4 |
| Phase 2 | 1 | Active not recruiting 1 |
Follow Ataxia: new trials by email Literature Review of Ataxia trials Research Report on Ataxia
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Study to Assess the Efficacy and Safety of Weekly Doses of GLM101 in Participants With PMM2-CDG GLM101 (Part A, Double-blind), Placebo (Part A, Double-blind), GLM101 (Part B, Open-label) - Phosphomannomutase 2 Deficiency, PMM2-CDG | Phase 2 / Phase 3 | Active not recruiting | Glycomine, Inc. | 50 | 2025-07-09 | 2026-08-14 |
| A Pivotal Study of N-Acetyl-L-Leucine on Ataxia-Telangiectasia (A-T) N-Acetyl-L-Leucine, Placebo - Ataxia-Telangiectasia, Ataxia-Telangiectasia (A-T) | Phase 3 | Active not recruiting | IntraBio Inc | 60 | 2025-03-18 | 2025-07-03 |
| Troriluzole in Adult Participants With Spinocerebellar Ataxia troriluzole, Placebo - Spinocerebellar Ataxias, Spinocerebellar Ataxia Type 1 | Phase 3 | Active not recruiting | Biohaven Pharmaceuticals, Inc. | 299 | 2019-03-08 | 2026-06-24 |
| Open Pilot Trial of BHV-4157 BHV-4157 - Spinocerebellar Ataxias, Spinocerebellar Ataxia Type 1 | Phase 3 | Active not recruiting | University of California, Los Angeles | 24 | 2017-12-15 | 2024-05-09 |
Machado-Joseph Disease (2) · Spinocerebellar Ataxias (2) · Ataxia Telangiectasia (1) · Congenital disorder of glycosylation type 1A (1) · Heart Arrest (1) · Spinocerebellar Ataxia 10 (1) · Spinocerebellar ataxia 8 (1)
Dyskinesias (4) · Nervous System Diseases (4) · Neurologic Manifestations (4) · Brain Diseases (3) · Central Nervous System Diseases (3) · Cerebellar Ataxia (3) · Cerebellar Diseases (3) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3) · Genetic Diseases, Inborn (3) · Cardiovascular Diseases (2) · Heredodegenerative Disorders, Nervous System (2) · Neurodegenerative Diseases (2) · Pathological Conditions, Signs and Symptoms (2) · Signs and Symptoms (2)
Double-Blind Method (1) · IB1001 (1) · acetylleucine (1)
Biohaven Pharmaceuticals, Inc. (1) · Glycomine, Inc. (1) · IntraBio Inc (1) · University of California, Los Angeles (1)
United States (4) · Germany (2) · Spain (2) · United Kingdom (2) · Belgium (1) · China (1) · Czechia (1) · France (1) · Italy (1) · Poland (1) · Portugal (1) · Slovakia (1) · Switzerland (1)