Alpha-Mannosidosis: Clinical Trials

1 trial for Alpha-Mannosidosis, newest first

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1 terminated. 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 31Terminated 1

Follow Alpha-Mannosidosis: new trials by email Literature Review of Alpha-Mannosidosis trials Research Report on Alpha-Mannosidosis

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
ALD-101 Adjuvant Therapy of Unrelated Umbilical Cord Blood Transfusion (UCBT) in Patients With Inherited Metabolic Diseases
ALD-101 - Inherited Metabolic Diseases, Lysosomal Storage Disorders
Phase 3TerminatedAldagen402008-03-012014-07-08

Narrower conditions

Adrenoleukodystrophy (1)  ·  Canavan Disease (1)  ·  Fucosidosis (1)  ·  Gangliosidosis, GM1 (1)  ·  Leukodystrophy, Globoid Cell (1)  ·  Leukodystrophy, Metachromatic (1)  ·  Lysosomal Storage Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Mucolipidoses (1)  ·  Mucopolysaccharidoses (1)  ·  Mucopolysaccharidosis I (1)  ·  Mucopolysaccharidosis II (1)  ·  Mucopolysaccharidosis III (1)  ·  Mucopolysaccharidosis VI (1)  ·  Sandhoff Disease (1)

Broader conditions

Adrenal Gland Diseases (1)  ·  Adrenal Insufficiency (1)  ·  Bone Diseases (1)  ·  Bone Diseases, Metabolic (1)  ·  Brain Diseases (1)  ·  Brain Diseases, Metabolic (1)  ·  Brain Diseases, Metabolic, Inborn (1)  ·  Carbohydrate Metabolism, Inborn Errors (1)  ·  Central Nervous System Diseases (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Connective Tissue Diseases (1)  ·  Death (1)  ·  Death, Sudden (1)  ·  Demyelinating Diseases (1)  ·  Endocrine System Diseases (1)

Sponsors

Aldagen (1)

Countries

United States (1)

Top investigators

James Hinson, MD (1)  ·  Joanne Kurtzberg, MD (1)