1 active not recruiting. 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Active not recruiting 1 |
| Phase 2 | 1 | Active not recruiting 1 |
Follow Wilson Disease: new trials by email Literature Review of Wilson Disease trials Research Report on Wilson Disease
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Phase 1/2/3 Study of UX701 Gene Therapy in Adults With Wilson Disease UX701, Standard of Care (SOC) - Wilson Disease | Phase 1 / Phase 2 | Active not recruiting | Ultragenyx Pharmaceutical Inc | 82 | 2021-09-27 | 2026-09-25 |
Hepatolenticular Degeneration (1)
Basal Ganglia Diseases (1) · Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Central Nervous System Diseases (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Digestive System Diseases (1) · Genetic Diseases, Inborn (1) · Heredodegenerative Disorders, Nervous System (1) · Liver Diseases (1) · Metabolic Diseases (1) · Metabolism, Inborn Errors (1) · Metal Metabolism, Inborn Errors (1) · Movement Disorders (1) · Nervous System Diseases (1)
Standard of Care (1)
Ultragenyx Pharmaceutical Inc (1)
Portugal (1) · Spain (1) · United Kingdom (1) · United States (1)