7 recruiting. 7 Phase 3, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 3 | 7 | Recruiting 7 |
| Phase 2 | 1 | Recruiting 1 |
Follow Urogenital Abnormalities: new trials by email Literature Review of Urogenital Abnormalities trials Research Report on Urogenital Abnormalities
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| The Efficacy and Safety of Inpegsomatropin Injection in Children With Turner Syndrome (TS) and Short Stature Inpegsomatropin-Injection, Givopegsomatropin Solution Injection - Turner Syndrome | Phase 3 | Recruiting | Xiamen Amoytop Biotech Co., Ltd. | 84 | 2026-07-05 | 2026-07-22 |
| A Study in Pediatric Participants With Congenital Adrenal Hyperplasia (Balance-CAH) Atumelnant, Placebo - Congenital Adrenal Hyperplasia, Classic Congenital Adrenal Hyperplasia | Phase 2 / Phase 3 | Recruiting | Crinetics Pharmaceuticals Inc. | 153 | 2026-01-22 | 2026-10-16 |
| Trial Investigating the Efficacy and Safety of Weekly Lonapegsomatropin Compared to Daily Somatropin in Children and Adolescents With Short Stature or Growth Failure Due to Growth Hormone Sufficient Disorders Lonapegsomatropin [SKYTROFA®], Somatropin Pen Injector - Turner Syndrome, Short Stature Homeobox Gene Mutation | Phase 3 | Recruiting | Ascendis Pharma A/S | 186 | 2025-12-12 | 2026-09-30 |
| A Study to Evaluate Atumelnant in Adults With Congenital Adrenal Hyperplasia Atumelnant, Placebo - Congenital Adrenal Hyperplasia, Classic Congenital Adrenal Hyperplasia | Phase 3 | Recruiting | Crinetics Pharmaceuticals Inc. | 150 | 2025-12-11 | 2026-10-16 |
| A Trial of Setmelanotide in Patients With Congenital Hypothalamic Obesity (Sub-study of NCT05774756) Setmelanotide, Placebo - Hypothalamic Obesity, Multiple Pituitary Hormone Deficiency Genetic Form | Phase 3 | Recruiting | Rhythm Pharmaceuticals, Inc. | 39 | 2025-09-23 | 2026-02-12 |
| Phase 3 Clinical Trial With Dapagliflozin in Chronic Kidney Disease in Adolescents and Young Adult Patients Dapagliflozin, Placebo - Chronic Kidney Failure in Children and Young Adults | Phase 3 | Recruiting | University Hospital Goettingen | 102 | 2024-03-25 | 2026-10-16 |
| Sex Steroids Balance for Metabolic and Reproductive Health in Klinefelter Syndrome Anastrozole, Semaglutide, human chorionic gonadotropin - Klinefelter Syndrome | Phase 3 | Recruiting | Georgios Papadakis | 150 | 2023-03-21 | 2026-05-11 |
Adrenal Hyperplasia, Congenital (2) · Turner Syndrome (2) · Chromosome Disorders (1) · Dwarfism (1) · Endocrine System Diseases (1) · Failure to Thrive (1) · Infertility (1) · Klinefelter Syndrome (1) · Metabolic Syndrome (1) · Nephritis, Hereditary (1) · Noonan Syndrome (1) · Optic Nerve Hypoplasia (1) · Septo-Optic Dysplasia (1) · Sex Chromosome Disorders (1) · Sex Chromosome Disorders of Sex Development (1)
Congenital Abnormalities (7) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (7) · Female Urogenital Diseases (7) · Female Urogenital Diseases and Pregnancy Complications (7) · Male Urogenital Diseases (7) · Urogenital Diseases (7) · Disorders of Sex Development (6) · Genetic Diseases, Inborn (6) · Gonadal Disorders (6) · Endocrine System Diseases (5) · Gonadal Dysgenesis (3) · Metabolic Diseases (3) · Nutritional and Metabolic Diseases (3) · Adrenal Gland Diseases (2)
Anastrozole (1) · Chorionic Gonadotropin (1) · dapagliflozin (1) · lonapegsomatropin (1) · semaglutide (1) · setmelanotide (1)
Crinetics Pharmaceuticals Inc. (2) · Ascendis Pharma A/S (1) · Georgios Papadakis (1) · Rhythm Pharmaceuticals, Inc. (1) · University Hospital Goettingen (1) · Xiamen Amoytop Biotech Co., Ltd. (1)
Germany (4) · United States (4) · France (3) · Italy (3) · United Kingdom (3) · Argentina (2) · Australia (2) · Brazil (2) · Netherlands (2) · Poland (2) · Saudi Arabia (2) · Austria (1) · Belgium (1) · Canada (1) · Chile (1)
David Meeker, MD (1) · Oliver Gross, MD (1) · Xiaoping Luo (1)
2023 (1)