Tuberous Sclerosis Complex: Clinical Trials

1 trial for Tuberous Sclerosis Complex, newest first

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1 not yet recruiting. 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 21Not yet recruiting 1

Follow Tuberous Sclerosis Complex: new trials by email Literature Review of Tuberous Sclerosis Complex trials Research Report on Tuberous Sclerosis Complex

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Safety and Efficacy of AV078 in Participants With Tuberous Sclerosis Complex (TSC) Refractory Epilepsy (RESTOR-1)
AV078, Placebo - Tuberous Sclerosis Complex, Epilepsy
Phase 2Not yet recruitingAeovian Pharmaceuticals, Inc.422026-09-012026-09-29

Narrower conditions

Drug Resistant Epilepsy (1)  ·  Epilepsy (1)  ·  Seizures (1)  ·  Tuberous Sclerosis (1)

Broader conditions

Brain Diseases (1)  ·  Central Nervous System Diseases (1)  ·  Congenital Abnormalities (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Hamartoma (1)  ·  Heredodegenerative Disorders, Nervous System (1)  ·  Malformations of Cortical Development (1)  ·  Malformations of Cortical Development, Group I (1)  ·  Neoplasms (1)  ·  Neoplasms, Multiple Primary (1)  ·  Neoplastic Syndromes, Hereditary (1)  ·  Nervous System Diseases (1)  ·  Nervous System Malformations (1)  ·  Neurocutaneous Syndromes (1)

Sponsors

Aeovian Pharmaceuticals, Inc. (1)

Countries

Canada (1)

NIH funding

2025 (1)