Thymidine Kinase 2 Deficiency: Clinical Trials

1 trial for Thymidine Kinase 2 Deficiency, newest first

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1 withdrawn. 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 31Withdrawn 1

Follow Thymidine Kinase 2 Deficiency: new trials by email Literature Review of Thymidine Kinase 2 Deficiency trials Research Report on Thymidine Kinase 2 Deficiency

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Study of the Efficacy and Safety of MT1621 in Thymidine Kinase 2 (TK2) Deficiency (Treatment naïve)
MT1621 - Thymidine Kinase 2 Deficiency
Phase 3WithdrawnZogenix MDS, Inc.2022-09-302023-09-01

Narrower conditions

Mitochondrial Diseases (1)  ·  Muscle Weakness (1)  ·  Muscular Atrophy (1)

Broader conditions

Atrophy (1)  ·  Metabolic Diseases (1)  ·  Muscular Diseases (1)  ·  Musculoskeletal Diseases (1)  ·  Nervous System Diseases (1)  ·  Neurologic Manifestations (1)  ·  Neuromuscular Manifestations (1)  ·  Nutritional and Metabolic Diseases (1)  ·  Pathologic Processes (1)  ·  Pathological Conditions, Anatomical (1)  ·  Pathological Conditions, Signs and Symptoms (1)  ·  Signs and Symptoms (1)

Interventions

Deoxycytidine (1)  ·  Thymidine (1)

Sponsors

Zogenix MDS, Inc. (1)