Reticular dysgenesis: Clinical Trials

3 trials for Reticular dysgenesis, newest first

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1 active not recruiting, 1 enrolling by invitation, 1 unknown. 1 Not applicable.

By phase and status

PhaseTrialsStatus
Not applicable1Active not recruiting 1

Follow Reticular dysgenesis: new trials by email Literature Review of Reticular dysgenesis trials Research Report on Reticular dysgenesis

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Allogeneic Hematopoietic Stem Cell Transplant for Patients With Primary Immune Deficiencies
Alemtuzumab 0.3 mg, Cyclophosphamide, Busulfan - SCID, Omenn's Syndrome
Not applicableActive not recruitingMasonic Cancer Center, University of Minnesota572012-09-042026-06-17
Patients Treated for SCID (1968-Present)
SCID, ADA-SCID
UnknownNational Institute of Allergy and Infectious Diseases (NIAID)10072011-05-152020-11-12
Natural History Study of SCID Disorders
Severe Combined Immunodeficiency (SCID), Leaky SCID
Enrolling by invitationNational Institute of Allergy and Infectious Diseases (NIAID)6902010-09-022020-11-10

Narrower conditions

Severe Combined Immunodeficiency (3)  ·  Severe combined immunodeficiency due to adenosine deaminase deficiency (2)  ·  X-Linked Combined Immunodeficiency Diseases (2)  ·  Chediak-Higashi Syndrome (1)  ·  Common Variable Immunodeficiency (1)  ·  Granulomatous Disease, Chronic (1)  ·  Histiocytosis, Langerhans-Cell (1)  ·  Hyper-IgM Immunodeficiency Syndrome (1)  ·  Immunologic Deficiency Syndromes (1)  ·  Lymphohistiocytosis, Hemophagocytic (1)  ·  Lymphoproliferative Disorders (1)  ·  Wiskott-Aldrich Syndrome (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3)  ·  DNA Repair-Deficiency Disorders (3)  ·  Genetic Diseases, Inborn (3)  ·  Genetic Diseases, X-Linked (3)  ·  Immune System Diseases (3)  ·  Infant, Newborn, Diseases (3)  ·  Metabolic Diseases (3)  ·  Nutritional and Metabolic Diseases (3)  ·  Primary Immunodeficiency Diseases (3)  ·  Immunologic Deficiency Syndromes (2)  ·  Albinism (1)  ·  Blood Coagulation Disorders (1)  ·  Blood Coagulation Disorders, Inherited (1)  ·  Blood Protein Disorders (1)  ·  Chronic Disease (1)

Interventions

Alemtuzumab (1)  ·  Busulfan (1)  ·  Cyclophosphamide (1)  ·  Melphalan (1)  ·  Mesna (1)  ·  Sodium (1)  ·  Stem Cell Transplantation (1)  ·  fludarabine phosphate (1)

Sponsors

National Institute of Allergy and Infectious Diseases (NIAID) (2)  ·  Masonic Cancer Center, University of Minnesota (1)

Countries

United States (3)  ·  Canada (2)

Top investigators

Morton J. Cowan, MD (2)  ·  Christopher C. Dvorak, MD (1)  ·  Elie Haddad, MD, PhD (1)  ·  Meera Srikanthan, MD (1)  ·  Richard J. O'Reilly, MD (1)

Results publications

PMID 20004776, PMID 23818196, PMID 24139498, PMID 24290292, PMID 24331379, PMID 25075835, PMID 27262745, PMID 30193840, PMID 35671392, PMID 41289158, PMID 29021228, PMID 29728406, PMID 30154114, PMID 30194989, PMID 33006109