Refractory Childhood Rhabdomyosarcoma: Clinical Trials

3 trials for Refractory Childhood Rhabdomyosarcoma, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

2 not yet recruiting, 1 active not recruiting. 3 Phase 2, 2 Phase 1.

By phase and status

PhaseTrialsStatus
Phase 23Not yet recruiting 2, Active not recruiting 1
Phase 12Not yet recruiting 2

Follow Refractory Childhood Rhabdomyosarcoma: new trials by email Literature Review of Refractory Childhood Rhabdomyosarcoma trials Research Report on Refractory Childhood Rhabdomyosarcoma

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Phase 1/2 Study of CBX-12 in Children, Adolescents, or Young Adults With Solid Tumors That Have Come Back After Treatment or Are Difficult to Treat
Archive Sample Retrieval, Biospecimen Collection, pH Low Insertion Peptide-exatecan Conjugate CBX-12 - Recurrent Childhood Ewing Sarcoma, Recurrent Childhood Malignant Solid Neoplasm
Phase 1 / Phase 2Not yet recruitingChildren's Oncology Group792027-05-072026-09-22
Testing the Addition of an Anti-Cancer Drug, Daraxonrasib, for Relapsed or Refractory Solid Tumors With RAS Mutations
Biospecimen Collection, Bone Marrow Aspiration, Bone Marrow Biopsy - Recurrent Childhood Malignant Solid Neoplasm, Recurrent Childhood Neuroblastoma
Phase 1 / Phase 2Not yet recruitingChildren's Oncology Group772027-04-092026-09-15
Erdafitinib in Treating Patients With Relapsed or Refractory Advanced Solid Tumors, Non-Hodgkin Lymphoma, or Histiocytic Disorders With FGFR Mutations (A Pediatric MATCH Treatment Trial)
Biospecimen Collection, Bone Marrow Aspiration and Biopsy, Bone Scan - Advanced Malignant Solid Neoplasm, Recurrent Childhood Ependymoma
Phase 2Active not recruitingNational Cancer Institute (NCI)202018-06-052026-10-16

Narrower conditions

Central Nervous System Neoplasms (1)  ·  Ependymoma (1)  ·  Familial ependymoma (1)  ·  Glioma (1)  ·  Hepatoblastoma (1)  ·  Histiocytosis, Langerhans-Cell (1)  ·  Lymphoma, Non-Hodgkin (1)  ·  Medulloblastoma (1)  ·  Neuroblastoma (1)  ·  Neuroectodermal Tumors, Primitive, Peripheral (1)  ·  Rhabdoid Tumor (1)  ·  Rhabdomyosarcoma (1)  ·  Sarcoma, Ewing (1)  ·  Wilms Tumor (1)

Broader conditions

Neoplasms (2)  ·  Neoplasms by Histologic Type (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Female Urogenital Diseases (1)  ·  Female Urogenital Diseases and Pregnancy Complications (1)  ·  Genetic Diseases, Inborn (1)  ·  Hemic and Lymphatic Diseases (1)  ·  Histiocytosis (1)  ·  Immune System Diseases (1)  ·  Immunoproliferative Disorders (1)  ·  Kidney Diseases (1)  ·  Kidney Neoplasms (1)  ·  Lung Diseases (1)  ·  Lung Diseases, Interstitial (1)  ·  Lymphatic Diseases (1)

Interventions

Specimen Handling (3)  ·  Biopsy (2)  ·  Phantoms, Imaging (2)  ·  X-Rays (2)  ·  Magnetic Resonance Spectroscopy (1)  ·  Nuclear Medicine Department, Hospital (1)  ·  erdafitinib (1)

Sponsors

Children's Oncology Group (2)  ·  National Cancer Institute (NCI) (1)

Countries

Puerto Rico (1)  ·  United States (1)

Top investigators

Alice Lee (1)  ·  Amit J Sabnis (1)  ·  Juan C Vasquez (1)

Results publications

PMID 31401903

NIH funding

UM1CA228823 (2), U10CA180886 (1), UM1CA081457 (1)