1 completed. 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Phase 3 | 1 | Completed 1 |
Follow Inherited Mitochondrial Disease: new trials by email Literature Review of Inherited Mitochondrial Disease trials Research Report on Inherited Mitochondrial Disease
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Safety Study for Previously Treated Vatiquinone (PTC743) Participants With Inherited Mitochondrial Disease Vatiquinone - Inherited Mitochondrial Disease | Phase 3 | Completed | PTC Therapeutics | 101 | 2022-06-22 | 2025-12-22 |
Diffuse Cerebral Sclerosis of Schilder (1) · Drug Resistant Epilepsy (1) · Leigh Disease (1) · MELAS Syndrome (1) · MERRF Syndrome (1) · Mitochondrial Encephalomyopathies (1)
Autoimmune Diseases (1) · Autoimmune Diseases of the Nervous System (1) · Brain Diseases (1) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Carbohydrate Metabolism, Inborn Errors (1) · Cardiovascular Diseases (1) · Central Nervous System Diseases (1) · Cerebral Small Vessel Diseases (1) · Cerebrovascular Disorders (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Demyelinating Autoimmune Diseases, CNS (1) · Demyelinating Diseases (1) · Epilepsies, Myoclonic (1) · Epilepsy (1)
PTC Therapeutics (1)
France (1) · Italy (1) · Japan (1) · Poland (1) · Spain (1) · United Kingdom (1) · United States (1)