Hemimegalencephaly: Clinical Trials

1 trial for Hemimegalencephaly, newest first

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1 recruiting. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Recruiting 1
Phase 21Recruiting 1

Follow Hemimegalencephaly: new trials by email Literature Review of Hemimegalencephaly trials Research Report on Hemimegalencephaly

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Safety, Tolerability, and Pharmacokinetics of SVG103 (Paxalisib) in Focal Cortical Dysplasia Type II (FCD-II), Tuberous Sclerosis Complex (TSC) or Hemimegalencephaly (HME)
SVG103 - Focal Cortical Dysplasia, Tuberous Sclerosis Complex (TSC)
Phase 1 / Phase 2RecruitingSovargen122026-07-142026-08-10

Narrower conditions

Focal Cortical Dysplasia (1)  ·  Tuberous Sclerosis (1)

Broader conditions

Congenital Abnormalities (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Craniofacial Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Hamartoma (1)  ·  Heredodegenerative Disorders, Nervous System (1)  ·  Malformations of Cortical Development (1)  ·  Malformations of Cortical Development, Group I (1)  ·  Megalencephaly (1)  ·  Musculoskeletal Abnormalities (1)  ·  Musculoskeletal Diseases (1)  ·  Neoplasms (1)  ·  Neoplasms, Multiple Primary (1)  ·  Neoplastic Syndromes, Hereditary (1)  ·  Nervous System Diseases (1)

Sponsors

Sovargen (1)

Countries

Australia (1)