3 recruiting, 2 completed, 1 active not recruiting. 2 Not applicable, 2 Phase 2, 1 Phase 1, 1 Phase 3.
| Phase | Trials | Status |
|---|---|---|
| Not applicable | 2 | Completed 1, Recruiting 1 |
| Phase 2 | 2 | Active not recruiting 1, Completed 1 |
| Phase 1 | 1 | Completed 1 |
| Phase 3 | 1 | Recruiting 1 |
Follow FSHD1: new trials by email Literature Review of FSHD1 trials Research Report on FSHD1
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Study to Evaluate Del-brax (Also Referred to as AOC 1020) in Participants With FSHD AOC-1020, Placebo - Facioscapulohumeral Muscular Dystrophy, FSHD | Phase 3 | Recruiting | Avidity Biosciences, Inc. | 200 | 2025-06-10 | 2026-07-27 |
| BetterLife FSHD: A Patient-driven Health and Research Platform Observational - FSH, FSH Muscular Dystrophy | Recruiting | FSHD Society | 5000 | 2024-08-02 | 2026-02-20 | |
| Phase 2 Open-label Extension Study of AOC 1020 in Participants With Facioscapulohumeral Muscular Dystrophy (FSHD) AOC 1020 - FSHD, FSHD1 | Phase 2 | Active not recruiting | Avidity Biosciences, Inc. | 84 | 2024-07-25 | 2026-07-14 |
| Longitudinal Study on Diaframmatic Ultrasound in FSHD Patients Diaphragmatic ultrasound, Pulmonary function test - FSHD1, FSHD2 | Not applicable | Recruiting | Fondazione Policlinico Universitario Agostino Gemelli IRCCS | 34 | 2023-07-18 | 2025-09-08 |
| Phase 1/2 Study of AOC 1020 in Participants With Facioscapulohumeral Muscular Dystrophy (FSHD) AOC 1020, Placebo - FSHD, FSHD1 | Phase 1 / Phase 2 | Completed | Avidity Biosciences, Inc. | 90 | 2023-04-04 | 2026-07-16 |
| Effect of Creatine Monohydrate on Functional Muscle Strength in Children With FSHD Creatine Monohydrate, Placebo - Facio-Scapulo-Humeral Dystrophy, FSHD2 | Not applicable | Completed | Murdoch Childrens Research Institute | 11 | 2017-10-31 | 2023-02-08 |
Muscular Dystrophy, Facioscapulohumeral (5) · Facioscapulohumeral Muscular Dystrophy 1B (4) · Facioscapulohumeral muscular dystrophy 1a (3) · Muscular Dystrophies (2)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (5) · Genetic Diseases, Inborn (5) · Muscular Diseases (5) · Muscular Disorders, Atrophic (5) · Musculoskeletal Diseases (5) · Nervous System Diseases (5) · Neuromuscular Diseases (5) · Muscular Dystrophies (3)
Sodium Chloride (2) · Creatine (1) · Respiratory Physiological Phenomena (1) · Watchful Waiting (1)
Avidity Biosciences, Inc. (3) · FSHD Society (1) · Fondazione Policlinico Universitario Agostino Gemelli IRCCS (1) · Murdoch Childrens Research Institute (1)
United States (4) · Canada (3) · United Kingdom (3) · Italy (2) · Australia (1) · Denmark (1) · France (1) · Germany (1) · Japan (1) · Netherlands (1) · Spain (1)
Amanda Hill, MBA (1) · Ian R Woodcock, MBBS (1) · Monique M Ryan (1) · Ricci Enzo (1)