1 completed. 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Completed 1 |
| Phase 2 | 1 | Completed 1 |
Follow FSHD1: new trials by email Literature Review of FSHD1 trials Research Report on FSHD1
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Phase 1/2 Study of AOC 1020 in Participants With Facioscapulohumeral Muscular Dystrophy (FSHD) AOC 1020, Placebo - FSHD, FSHD1 | Phase 1 / Phase 2 | Completed | Avidity Biosciences, Inc. | 90 | 2023-04-04 | 2026-07-16 |
Facioscapulohumeral Muscular Dystrophy 1B (1) · Facioscapulohumeral muscular dystrophy 1a (1) · Muscular Dystrophies (1) · Muscular Dystrophy, Facioscapulohumeral (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Muscular Diseases (1) · Muscular Disorders, Atrophic (1) · Musculoskeletal Diseases (1) · Nervous System Diseases (1) · Neuromuscular Diseases (1)
Sodium Chloride (1)
Canada (1) · United Kingdom (1) · United States (1)