FSHD1: Clinical Trials

1 trial for FSHD1, newest first

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1 completed. 1 Phase 1, 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 11Completed 1
Phase 21Completed 1

Follow FSHD1: new trials by email Literature Review of FSHD1 trials Research Report on FSHD1

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Phase 1/2 Study of AOC 1020 in Participants With Facioscapulohumeral Muscular Dystrophy (FSHD)
AOC 1020, Placebo - FSHD, FSHD1
Phase 1 / Phase 2CompletedAvidity Biosciences, Inc.902023-04-042026-07-16

Narrower conditions

Facioscapulohumeral Muscular Dystrophy 1B (1)  ·  Facioscapulohumeral muscular dystrophy 1a (1)  ·  Muscular Dystrophies (1)  ·  Muscular Dystrophy, Facioscapulohumeral (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Muscular Diseases (1)  ·  Muscular Disorders, Atrophic (1)  ·  Musculoskeletal Diseases (1)  ·  Nervous System Diseases (1)  ·  Neuromuscular Diseases (1)

Interventions

Sodium Chloride (1)

Sponsors

Avidity Biosciences, Inc. (1)

Countries

Canada (1)  ·  United Kingdom (1)  ·  United States (1)