FSHD1: Clinical Trials

2 trials for FSHD1, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

1 completed, 1 recruiting. 2 Not applicable.

By phase and status

PhaseTrialsStatus
Not applicable2Completed 1, Recruiting 1

Follow FSHD1: new trials by email Literature Review of FSHD1 trials Research Report on FSHD1

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Longitudinal Study on Diaframmatic Ultrasound in FSHD Patients
Diaphragmatic ultrasound, Pulmonary function test - FSHD1, FSHD2
Not applicableRecruitingFondazione Policlinico Universitario Agostino Gemelli IRCCS342023-07-182025-09-08
Effect of Creatine Monohydrate on Functional Muscle Strength in Children With FSHD
Creatine Monohydrate, Placebo - Facio-Scapulo-Humeral Dystrophy, FSHD2
Not applicableCompletedMurdoch Childrens Research Institute112017-10-312023-02-08

Narrower conditions

Muscular Dystrophy, Facioscapulohumeral (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Muscular Diseases (1)  ·  Muscular Disorders, Atrophic (1)  ·  Muscular Dystrophies (1)  ·  Musculoskeletal Diseases (1)  ·  Nervous System Diseases (1)  ·  Neuromuscular Diseases (1)

Interventions

Creatine (1)  ·  Respiratory Physiological Phenomena (1)

Sponsors

Fondazione Policlinico Universitario Agostino Gemelli IRCCS (1)  ·  Murdoch Childrens Research Institute (1)

Countries

Australia (1)  ·  Italy (1)

Top investigators

Ian R Woodcock, MBBS (1)  ·  Monique M Ryan (1)  ·  Ricci Enzo (1)

Results publications

PMID 40366059