1 completed, 1 recruiting. 2 Not applicable.
| Phase | Trials | Status |
|---|---|---|
| Not applicable | 2 | Completed 1, Recruiting 1 |
Follow FSHD1: new trials by email Literature Review of FSHD1 trials Research Report on FSHD1
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Longitudinal Study on Diaframmatic Ultrasound in FSHD Patients Diaphragmatic ultrasound, Pulmonary function test - FSHD1, FSHD2 | Not applicable | Recruiting | Fondazione Policlinico Universitario Agostino Gemelli IRCCS | 34 | 2023-07-18 | 2025-09-08 |
| Effect of Creatine Monohydrate on Functional Muscle Strength in Children With FSHD Creatine Monohydrate, Placebo - Facio-Scapulo-Humeral Dystrophy, FSHD2 | Not applicable | Completed | Murdoch Childrens Research Institute | 11 | 2017-10-31 | 2023-02-08 |
Muscular Dystrophy, Facioscapulohumeral (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Muscular Diseases (1) · Muscular Disorders, Atrophic (1) · Muscular Dystrophies (1) · Musculoskeletal Diseases (1) · Nervous System Diseases (1) · Neuromuscular Diseases (1)
Creatine (1) · Respiratory Physiological Phenomena (1)
Fondazione Policlinico Universitario Agostino Gemelli IRCCS (1) · Murdoch Childrens Research Institute (1)
Australia (1) · Italy (1)
Ian R Woodcock, MBBS (1) · Monique M Ryan (1) · Ricci Enzo (1)