1 recruiting, 1 unknown. 2 Phase 2, 1 Phase 1.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 2 | Recruiting 1, Unknown 1 |
| Phase 1 | 1 | Recruiting 1 |
Follow Cone-Rod Dystrophy: new trials by email Literature Review of Cone-Rod Dystrophy trials Research Report on Cone-Rod Dystrophy
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Study to Investigate the Safety of OpCT-001 in Adults Who Have Primary Photoreceptor Disease (CLARICO) OpCT-001 - Primary Photoreceptor Disease, Retinitis Pigmentosa (RP) | Phase 1 / Phase 2 | Recruiting | BlueRock Therapeutics | 54 | 2025-03-10 | 2026-10-15 |
| Cholesterol and Antioxidant Treatment in Patients With Smith-Lemli-Opitz Syndrome (SLOS) Antioxidants, Cholesterol - Smith-Lemli-Opitz Syndrome, Cone-Rod Dystrophy | Phase 2 | Unknown | University of Colorado, Denver | 100 | 2008-12-01 | 2024-05-08 |
Cone-Rod Dystrophies (2) · Hearing Loss (1) · Retinal Degeneration (1) · Retinitis Pigmentosa (1) · Smith-Lemli-Opitz Syndrome (1) · Usher Syndromes (1)
Abnormalities, Multiple (2) · Congenital Abnormalities (2) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Ear Diseases (2) · Eye Diseases (2) · Eye Diseases, Hereditary (2) · Genetic Diseases, Inborn (2) · Hearing Disorders (2) · Nervous System Diseases (2) · Neurologic Manifestations (2) · Otorhinolaryngologic Diseases (2) · Pathological Conditions, Signs and Symptoms (2) · Retinal Diseases (2) · Retinal Dystrophies (2) · Sensation Disorders (2)
Antioxidants (1) · Cholesterol (1) · Eggs (1)
BlueRock Therapeutics (1) · University of Colorado, Denver (1)
United States (2)