Cohen syndrome: Clinical Trials

2 trials for Cohen syndrome, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

1 completed, 1 recruiting. 1 Phase 3.

By phase and status

PhaseTrialsStatus
Phase 31Recruiting 1

Follow Cohen syndrome: new trials by email Literature Review of Cohen syndrome trials Research Report on Cohen syndrome

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Study of Mavorixafor in Participants With Congenital and Acquired Primary Autoimmune and Idiopathic Chronic Neutropenic Disorders Who Are Experiencing Recurrent and/or Serious Infections
Mavorixafor, Placebo - Neutropenia
Phase 3RecruitingX4 Pharmaceuticals1762024-06-062026-08-06
Clinical, Molecular and Physiopathological Study of Cohen Syndrome and Cohen-like Syndromes
Cohen Syndrome
CompletedCentre Hospitalier Universitaire Dijon1002013-07-242018-01-31

Narrower conditions

Autoimmune Diseases (1)  ·  Barth Syndrome (1)  ·  Neutropenia (1)  ·  Neutropenia, Severe Congenital, Autosomal Recessive 3 (1)  ·  Shwachman-Diamond Syndrome (1)

Broader conditions

Abnormalities, Multiple (1)  ·  Agranulocytosis (1)  ·  Bone Marrow Diseases (1)  ·  Bone Marrow Failure Disorders (1)  ·  Cardiovascular Abnormalities (1)  ·  Cardiovascular Diseases (1)  ·  Congenital Abnormalities (1)  ·  Congenital Bone Marrow Failure Syndromes (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Cytopenia (1)  ·  Digestive System Diseases (1)  ·  Exocrine Pancreatic Insufficiency (1)  ·  Genetic Diseases, Inborn (1)  ·  Genetic Diseases, X-Linked (1)  ·  Heart Defects, Congenital (1)

Interventions

mavorixafor (1)

Sponsors

Centre Hospitalier Universitaire Dijon (1)  ·  X4 Pharmaceuticals (1)

Countries

France (2)  ·  Argentina (1)  ·  Australia (1)  ·  Belgium (1)  ·  Canada (1)  ·  Colombia (1)  ·  Czechia (1)  ·  Georgia (1)  ·  Germany (1)  ·  Greece (1)  ·  Hungary (1)  ·  India (1)  ·  Israel (1)  ·  Italy (1)  ·  Malaysia (1)

NIH funding

2023 (1)