4 completed, 1 recruiting, 1 terminated, 1 unknown. 7 Phase 1, 4 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 7 | Completed 4, Recruiting 1, Terminated 1, Unknown 1 |
| Phase 2 | 4 | Completed 3, Terminated 1 |
Follow Albinism: new trials by email Literature Review of Albinism trials Research Report on Albinism
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Study of the c-Kit Specific Antibody-Drug Conjugate NN3201 for Advanced and/or Metastatic Solid Tumors Known to Express c-Kit NN3201 - Gastrointestinal Stromal Tumors, Small-cell Lung Cancer | Phase 1 | Recruiting | Novelty Nobility, Inc. | 67 | 2025-02-03 | 2026-11-13 |
| Japanese OMI Treatment With Kit-positive Cells for Enhanced Regeneration Stem cells administered to participants - Chronic Heart Failure, Old Myocardial Infarction | Phase 1 | Unknown | Sakakibara Heart Institute | 6 | 2017-11-15 | 2021-03-18 |
| Bone Marrow Transplant With Abatacept for Non-Malignant Diseases Abatacept - Hurler Syndrome, Fanconi Anemia | Phase 1 | Completed | Emory University | 10 | 2014-01-01 | 2019-12-26 |
| Nitisinone for Type 1B Oculocutaneous Albinism Nitisinone - Albinism, Vision Loss | Phase 1 / Phase 2 | Completed | National Eye Institute (NEI) | 5 | 2013-04-16 | 2019-02-26 |
| Unrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood Cells Hematopoietic stem cell transplantation - Sickle Cell Disease, Thalassemia | Phase 1 / Phase 2 | Completed | Children's Hospital Los Angeles | 25 | 2008-08-01 | 2016-06-23 |
| Pilot Study of a Multi-Drug Regimen for Severe Pulmonary Fibrosis in Hermansky-Pudlak Syndrome Losartan, Zileuton, N-Acetylcysteine - Hermansky-Pudlak Syndrome (HPS), Pulmonary Fibrosis | Phase 1 / Phase 2 | Terminated | National Human Genome Research Institute (NHGRI) | 3 | 2007-04-01 | 2013-08-02 |
| A Study of Imatinib With Reinduction Chemotherapy Using Mitoxantrone, Etoposide and Cytarabine in Patients With Relapsed/Refractory C-kit Positive (AML) Acute Myeloid Leukemia Imatinib (Gleevec) - Leukemia | Phase 1 / Phase 2 | Completed | University Health Network, Toronto | 35 | 2004-07-01 | 2015-06-24 |
Piebaldism (3) · Anemia, Sickle Cell (2) · Chediak-Higashi Syndrome (2) · Granulomatous Disease, Chronic (2) · Mucopolysaccharidosis I (2) · Neutropenia, Severe Congenital, Autosomal Recessive 3 (2) · Wiskott-Aldrich Syndrome (2) · Albinism, Oculocutaneous (1) · Anemia (1) · Anemia, Aplastic (1) · Anemia, Diamond-Blackfan (1) · Anemia, Dyserythropoietic, Congenital (1) · Carcinoma, Adenoid Cystic (1) · Carcinoma, Renal Cell (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (7) · Eye Diseases, Hereditary (7) · Metabolism, Inborn Errors (7) · Nutritional and Metabolic Diseases (7) · Skin and Connective Tissue Diseases (7) · Genetic Diseases, Inborn (6) · Metabolic Diseases (6) · Skin Diseases (6) · Skin Diseases, Genetic (6) · Amino Acid Metabolism, Inborn Errors (5) · Eye Diseases (5) · Hypopigmentation (5) · Pigmentation Disorders (5) · Hematologic Diseases (4)
Abatacept (1) · Acetylcysteine (1) · Erythromycin (1) · Hematopoietic Stem Cell Transplantation (1) · Imatinib Mesylate (1) · Losartan (1) · Pravastatin (1) · nitisinone (1) · zileuton (1)
Children's Hospital Los Angeles (1) · Emory University (1) · National Eye Institute (NEI) (1) · National Human Genome Research Institute (NHGRI) (1) · Novelty Nobility, Inc. (1) · Sakakibara Heart Institute (1) · University Health Network, Toronto (1)
United States (5) · Canada (1) · Japan (1)
Brian P Brooks, M.D. (1) · Hisham Abdel-Azim, MD (1) · John T Horan, MD (1) · Sunil Sharma, MD (1) · Thomas Markello, M.D. (1)