Wilson Disease: Clinical Trials

3 trials for Wilson Disease, newest first

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3 completed. 3 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 23Completed 3

Follow Wilson Disease: new trials by email Literature Review of Wilson Disease trials Research Report on Wilson Disease

Trials (filtered) newest first · largest first

All 3 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Copper Concentration & Histopathologic Changes in Liver Biopsy in Participants With Wilson Disease Treated With ALXN1840
Bis-Choline Tetrathiomolybdate - Wilson Disease
Phase 2CompletedAlexion Pharmaceuticals, Inc.312020-12-022024-10-18
Copper and Molybdenum Balance in Participants With Wilson Disease Treated With ALXN1840
ALXN1840 - Wilson Disease
Phase 2CompletedAlexion Pharmaceuticals, Inc.92020-09-072024-06-24
Efficacy and Safety Study of WTX101 (ALXN1840) in Adult Wilson Disease Patients
ALXN1840 - Wilson Disease
Phase 2CompletedAlexion Pharmaceuticals, Inc.292014-11-242021-09-29

Narrower conditions

Hepatolenticular Degeneration (3)

Broader conditions

Basal Ganglia Diseases (3)  ·  Brain Diseases (3)  ·  Brain Diseases, Metabolic (3)  ·  Brain Diseases, Metabolic, Inborn (3)  ·  Central Nervous System Diseases (3)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3)  ·  Digestive System Diseases (3)  ·  Genetic Diseases, Inborn (3)  ·  Heredodegenerative Disorders, Nervous System (3)  ·  Liver Diseases (3)  ·  Metabolic Diseases (3)  ·  Metabolism, Inborn Errors (3)  ·  Metal Metabolism, Inborn Errors (3)  ·  Movement Disorders (3)  ·  Nervous System Diseases (3)

Interventions

tetrathiomolybdate (1)

Sponsors

Alexion Pharmaceuticals, Inc. (3)

Countries

United Kingdom (3)  ·  United States (3)  ·  New Zealand (2)  ·  Austria (1)  ·  Canada (1)  ·  Denmark (1)  ·  Germany (1)  ·  Poland (1)  ·  Russia (1)  ·  Singapore (1)  ·  Spain (1)

Top investigators

Eugene S. Swenson, MD, PhD (2)  ·  Eugene Swenson, MD, PhD (1)  ·  Peter Ksenuk, MD (1)

Results publications

PMID 28988934

NIH funding

2019 (1)