1 enrolling by invitation, 1 recruiting. 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Enrolling by invitation 1 |
| Phase 2 | 1 | Enrolling by invitation 1 |
Follow WHIM: new trials by email Literature Review of WHIM trials Research Report on WHIM
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Base-Edited Hematopoietic Stem/Progenitor Cell Gene Therapy for Treatment of CXCR4-WHIM Busulfan, Palifermin, Plerixafor - WHIM, Warts | Phase 1 / Phase 2 | Enrolling by invitation | National Institute of Allergy and Infectious Diseases (NIAID) | 10 | 2026-10-27 | 2026-10-22 |
| Shwachman-Diamond Syndrome Global Patient Survey and Partnering Platform Shwachman-Diamond Syndrome, SDS | Recruiting | Shwachman-Diamond Syndrome Alliance Inc | 8000 | 2024-02-07 | 2025-05-31 |
Immunologic Deficiency Syndromes (2) · Agammaglobulinemia (1) · Congenital Bone Marrow Failure Syndromes (1) · Exocrine Pancreatic Insufficiency (1) · Lymphoma, Follicular (1) · Myelodysplastic Syndromes (1) · Neoplastic Syndromes, Hereditary (1) · Neutropenia, Severe Congenital, Autosomal Recessive 3 (1) · Neutropenia, severe chronic (1) · Pancytopenia (1) · Primary Immunodeficiency Diseases (1) · Shwachman-Diamond Syndrome (1) · Warts (1)
Hematologic Diseases (2) · Hemic and Lymphatic Diseases (2) · Immune System Diseases (2) · Lymphatic Diseases (2) · Lymphoproliferative Disorders (2) · Blood Protein Disorders (1) · Bone Marrow Diseases (1) · Bone Marrow Failure Disorders (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Cytopenia (1) · DNA Virus Infections (1) · Digestive System Diseases (1) · Genetic Diseases, Inborn (1) · Immunoproliferative Disorders (1) · Infant, Newborn, Diseases (1)
Busulfan (1) · Fibroblast Growth Factor 7 (1) · Filgrastim (1) · plerixafor (1)
National Institute of Allergy and Infectious Diseases (NIAID) (1) · Shwachman-Diamond Syndrome Alliance Inc (1)
United States (2)