Thymidine Kinase 2 Deficiency: Clinical Trials

1 trial for Thymidine Kinase 2 Deficiency, newest first

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1 completed. 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 21Completed 1

Follow Thymidine Kinase 2 Deficiency: new trials by email Literature Review of Thymidine Kinase 2 Deficiency trials Research Report on Thymidine Kinase 2 Deficiency

Trials (filtered) newest first · largest first

All 1 trial

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
An Open-Label Study of Continuation Treatment With Combination Pyrimidine Nucleosides in Patients With TK2 Deficiency
doxecitine and doxribtimine - Thymidine Kinase 2 Deficiency
Phase 2CompletedUCB BIOSCIENCES, Inc.472019-07-052026-09-08

Narrower conditions

Mitochondrial Diseases (1)  ·  Muscle Weakness (1)  ·  Muscular Atrophy (1)

Broader conditions

Atrophy (1)  ·  Metabolic Diseases (1)  ·  Muscular Diseases (1)  ·  Musculoskeletal Diseases (1)  ·  Nervous System Diseases (1)  ·  Neurologic Manifestations (1)  ·  Neuromuscular Manifestations (1)  ·  Nutritional and Metabolic Diseases (1)  ·  Pathologic Processes (1)  ·  Pathological Conditions, Anatomical (1)  ·  Pathological Conditions, Signs and Symptoms (1)  ·  Signs and Symptoms (1)

Interventions

Deoxycytidine (1)  ·  Thymidine (1)

Sponsors

UCB BIOSCIENCES, Inc. (1)

Countries

Israel (1)  ·  Spain (1)  ·  United States (1)

Results publications

PMID 33246973

NIH funding

2018 (1), 2023 (1)