1 completed. 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 2 | 1 | Completed 1 |
Follow Thymidine Kinase 2 Deficiency: new trials by email Literature Review of Thymidine Kinase 2 Deficiency trials Research Report on Thymidine Kinase 2 Deficiency
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| An Open-Label Study of Continuation Treatment With Combination Pyrimidine Nucleosides in Patients With TK2 Deficiency doxecitine and doxribtimine - Thymidine Kinase 2 Deficiency | Phase 2 | Completed | UCB BIOSCIENCES, Inc. | 47 | 2019-07-05 | 2026-09-08 |
Mitochondrial Diseases (1) · Muscle Weakness (1) · Muscular Atrophy (1)
Atrophy (1) · Metabolic Diseases (1) · Muscular Diseases (1) · Musculoskeletal Diseases (1) · Nervous System Diseases (1) · Neurologic Manifestations (1) · Neuromuscular Manifestations (1) · Nutritional and Metabolic Diseases (1) · Pathologic Processes (1) · Pathological Conditions, Anatomical (1) · Pathological Conditions, Signs and Symptoms (1) · Signs and Symptoms (1)
Deoxycytidine (1) · Thymidine (1)
Israel (1) · Spain (1) · United States (1)
2018 (1), 2023 (1)