SPG4: Clinical Trials

3 trials for SPG4, newest first

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2 recruiting, 1 completed. .

Follow SPG4: new trials by email Literature Review of SPG4 trials Research Report on SPG4

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Spastic Paraplegia - Centers of Excellence Research Network
Hereditary Spastic Paraplegia, Primary Lateral Sclerosis
RecruitingBoston Children's Hospital1002024-06-042026-03-18
Registry and Natural History Study for Early Onset Hereditary Spastic Paraplegia
Hereditary Spastic Paraplegia, SPG47
RecruitingBoston Children's Hospital7002020-04-272026-03-18
Studying Non-motor Symptoms in HSP
EuroQol five dimensions questionaire (EQ-5D), Modified Fatigue Impact Scale (MFI), Brief Pain Inventory (BPI) - SPG4
CompletedUniversity Hospital Tuebingen2362018-04-282020-08-27

Narrower conditions

Spastic Paraplegia, Hereditary (2)  ·  Motor Neuron Disease (1)  ·  Neuromuscular Diseases (1)  ·  Paraplegia (1)  ·  Spastic Paraplegia Type 4 (1)  ·  Spastic paraplegia 3, autosomal dominant (1)

Broader conditions

Congenital Abnormalities (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Genetic Diseases, Inborn (2)  ·  Hereditary Sensory and Motor Neuropathy (2)  ·  Heredodegenerative Disorders, Nervous System (2)  ·  Nervous System Diseases (2)  ·  Nervous System Malformations (2)  ·  Neurodegenerative Diseases (2)  ·  Peripheral Nervous System Diseases (2)  ·  Polyneuropathies (2)  ·  Neurologic Manifestations (1)  ·  Neuromuscular Diseases (1)  ·  Paralysis (1)  ·  Pathological Conditions, Signs and Symptoms (1)  ·  Signs and Symptoms (1)

Sponsors

Boston Children's Hospital (2)  ·  University Hospital Tuebingen (1)

Countries

United States (2)  ·  Germany (1)

Top investigators

Tim W. Rattay, MD (1)

Results publications

PMID 31646384, PMID 41199121, PMID 41491634