Leukodystrophy, Globoid Cell: Clinical Trials

1 trial for Leukodystrophy, Globoid Cell, newest first

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1 completed. 1 Not applicable.

By phase and status

PhaseTrialsStatus
Not applicable1Completed 1

Follow Leukodystrophy, Globoid Cell: new trials by email Literature Review of Leukodystrophy, Globoid Cell trials Research Report on Leukodystrophy, Globoid Cell

Trials (filtered) newest first · largest first

All 1 trial

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TrialPhaseStatusSponsorEnrollmentStartUpdated
Reduced-Intensity Hematopoietic Stem Cell Transplant for High Risk Lysosomal and Peroxisomal Disorders
Campath-1H, Clofarabine, Melphalan - Lysosomal Storage Disease, Peroxisomal Disorder
Not applicableCompletedMasonic Cancer Center, University of Minnesota32012-07-112017-12-05

Narrower conditions

Adrenoleukodystrophy (1)  ·  Gangliosidosis, GM1 (1)  ·  Leukodystrophy, Metachromatic (1)  ·  Lysosomal Storage Diseases (1)  ·  Mucolipidoses (1)  ·  Mucopolysaccharidosis III (1)  ·  Peroxisomal Disorders (1)  ·  Sandhoff Disease (1)  ·  Tay-Sachs Disease (1)  ·  Wolman Disease (1)

Broader conditions

Adrenal Gland Diseases (1)  ·  Adrenal Insufficiency (1)  ·  Bone Diseases (1)  ·  Bone Diseases, Metabolic (1)  ·  Brain Diseases (1)  ·  Brain Diseases, Metabolic (1)  ·  Brain Diseases, Metabolic, Inborn (1)  ·  Carbohydrate Metabolism, Inborn Errors (1)  ·  Central Nervous System Diseases (1)  ·  Cholesterol Ester Storage Disease (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Connective Tissue Diseases (1)  ·  Demyelinating Diseases (1)  ·  Endocrine System Diseases (1)  ·  Gangliosidoses (1)

Interventions

Alemtuzumab (1)  ·  Clofarabine (1)  ·  Cyclosporine (1)  ·  Hematopoietic Stem Cell Transplantation (1)  ·  Melphalan (1)  ·  Mycophenolic Acid (1)  ·  Radiotherapy, Intensity-Modulated (1)  ·  Whole-Body Irradiation (1)

Sponsors

Masonic Cancer Center, University of Minnesota (1)

Countries

United States (1)

Top investigators

Weston Miller, MD (1)