1 recruiting. 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Recruiting 1 |
| Phase 2 | 1 | Recruiting 1 |
Follow Lafora Disease: new trials by email Literature Review of Lafora Disease trials Research Report on Lafora Disease
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Safety and Efficacy of Intrathecally Administered ION283 in Patients With Lafora Disease ION283 - Lafora Disease | Phase 1 / Phase 2 | Recruiting | Berge Minassian | 10 | 2024-12-03 | 2025-12-18 |
Brain Diseases (1) · Central Nervous System Diseases (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Epilepsies, Myoclonic (1) · Epilepsy (1) · Epilepsy, Generalized (1) · Epileptic Syndromes (1) · Genetic Diseases, Inborn (1) · Heredodegenerative Disorders, Nervous System (1) · Myoclonic Epilepsies, Progressive (1) · Nervous System Diseases (1) · Neurodegenerative Diseases (1)
Berge Minassian (1)
United States (1)