1 recruiting. 1 Phase 1, 1 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 1 | Recruiting 1 |
| Phase 2 | 1 | Recruiting 1 |
Follow Intellectual Deficiency: new trials by email Literature Review of Intellectual Deficiency trials Research Report on Intellectual Deficiency
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Melpida: Recombinant Adeno-associated Virus (Serotype 9) Encoding a Codon Optimized Human AP4M1 Transgene (hAP4M1opt) MELPIDA - Spasticity, Muscle, Microcephaly | Phase 1 / Phase 2 | Recruiting | Elpida Therapeutics SPC | 4 | 2023-02-15 | 2026-07-08 |
Microcephaly (1) · Muscle Spasticity (1) · Paraplegia (1)
Congenital Abnormalities (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Craniofacial Abnormalities (1) · Malformations of Cortical Development (1) · Malformations of Cortical Development, Group I (1) · Muscle Hypertonia (1) · Muscular Diseases (1) · Musculoskeletal Abnormalities (1) · Musculoskeletal Diseases (1) · Nervous System Diseases (1) · Nervous System Malformations (1) · Neurologic Manifestations (1) · Neuromuscular Manifestations (1) · Paralysis (1) · Pathological Conditions, Signs and Symptoms (1)
United States (1)
Susan T. Iannaccone, MD, FAAN (1)