1 recruiting. .
Follow GSD X: new trials by email Literature Review of GSD X trials Research Report on GSD X
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Rare Glycogen Storage Diseases Natural History Study No intervention - Glycogen Storage Disease, GSD Type 0A | Recruiting | Duke University | 200 | 2024-12-23 | 2026-01-07 |
Dimauro disease (1) · Glycogen Storage Disease (1) · Glycogen Storage Disease Type IIb (1) · Glycogen Storage Disease Type VII (1) · Glycogen Storage Disease XII (1) · Glycogen Storage Disease XIII (1)
Carbohydrate Metabolism, Inborn Errors (1) · Cardiomyopathies (1) · Cardiovascular Diseases (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Genetic Diseases, X-Linked (1) · Heart Diseases (1) · Intellectual Disability (1) · Metabolic Diseases (1) · Metabolism, Inborn Errors (1) · Muscular Diseases (1) · Muscular Disorders, Atrophic (1) · Muscular Dystrophies (1) · Musculoskeletal Diseases (1) · Nervous System Diseases (1)
Duke University (1)
United States (1)