GSD X: Clinical Trials

1 trial for GSD X, newest first

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1 recruiting. .

Follow GSD X: new trials by email Literature Review of GSD X trials Research Report on GSD X

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Rare Glycogen Storage Diseases Natural History Study
No intervention - Glycogen Storage Disease, GSD Type 0A
RecruitingDuke University2002024-12-232026-01-07

Narrower conditions

Dimauro disease (1)  ·  Glycogen Storage Disease (1)  ·  Glycogen Storage Disease Type IIb (1)  ·  Glycogen Storage Disease Type VII (1)  ·  Glycogen Storage Disease XII (1)  ·  Glycogen Storage Disease XIII (1)

Broader conditions

Carbohydrate Metabolism, Inborn Errors (1)  ·  Cardiomyopathies (1)  ·  Cardiovascular Diseases (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Genetic Diseases, X-Linked (1)  ·  Heart Diseases (1)  ·  Intellectual Disability (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Muscular Diseases (1)  ·  Muscular Disorders, Atrophic (1)  ·  Muscular Dystrophies (1)  ·  Musculoskeletal Diseases (1)  ·  Nervous System Diseases (1)

Sponsors

Duke University (1)

Countries

United States (1)

Top investigators

Priya Kishnani, M.D. (1)