Fahr's disease: Clinical Trials

2 trials for Fahr's disease, newest first

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2 recruiting. 1 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 21Recruiting 1

Follow Fahr's disease: new trials by email Literature Review of Fahr's disease trials Research Report on Fahr's disease

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Treatment of Ectopic Calcification in Fahr's Disease or Syndrome
Etidronate, Placebo - Fahr Disease, Fahr Syndrome
Phase 2RecruitingUMC Utrecht982023-04-032026-03-02
Longitudinal Study of Ultra-rare Inherited Metabolic and Degenerative Neurological Diseases.
collection of data - Inherited Disease, Rare Diseases
RecruitingFondazione I.R.C.C.S. Istituto Neurologico Carlo Besta1002021-03-012026-11-06

Narrower conditions

2-Hydroxyglutaricaciduria (1)  ·  Adrenoleukodystrophy (1)  ·  Alexander Disease (1)  ·  Cysts (1)  ·  Genetic Diseases, Inborn (1)  ·  Hepatolenticular Degeneration (1)  ·  Leukodystrophy, Globoid Cell (1)  ·  Leukodystrophy, Metachromatic (1)  ·  Leukoencephalopathies (1)  ·  Metabolic Diseases (1)  ·  Methylmalonic acidemia with homocystinuria (1)  ·  Nervous System Diseases (1)  ·  Pelizaeus-Merzbacher Disease (1)  ·  Polycystic lipomembranous osteodysplasia with sclerosing leukoencephalopathy (1)

Broader conditions

Adrenal Gland Diseases (1)  ·  Adrenal Insufficiency (1)  ·  Basal Ganglia Diseases (1)  ·  Brain Diseases (1)  ·  Brain Diseases, Metabolic (1)  ·  Brain Diseases, Metabolic, Inborn (1)  ·  Central Nervous System Diseases (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Demyelinating Diseases (1)  ·  Digestive System Diseases (1)  ·  Disease Attributes (1)  ·  Endocrine System Diseases (1)  ·  Genetic Diseases, X-Linked (1)  ·  Hereditary Central Nervous System Demyelinating Diseases (1)  ·  Heredodegenerative Disorders, Nervous System (1)

Interventions

Etidronic Acid (1)

Sponsors

Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta (1)  ·  UMC Utrecht (1)

Countries

Italy (1)  ·  Netherlands (1)  ·  United Kingdom (1)

Top investigators

Huiberdina L Koek, MD, PhD (1)

Results publications

PMID 37782421, PMID 38326858, PMID 41667276