5 unknown, 2 recruiting, 1 active not recruiting. 1 Not applicable.
| Phase | Trials | Status |
|---|---|---|
| Not applicable | 1 | Unknown 1 |
Follow Fabry Disease, Cardiac Variant: new trials by email Literature Review of Fabry Disease, Cardiac Variant trials Research Report on Fabry Disease, Cardiac Variant
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| CVI Alterations in FD: a Prospective, Multicenter, Observational Cohort Study Fabry Disease, Cardiac Variant | Recruiting | China National Center for Cardiovascular Diseases | 300 | 2024-12-31 | 2025-03-26 | |
| Molecular Imaging in Fabry Disease of the Heart 68Ga-DOTATATE PET/MRI - Fabry Disease, Cardiac Variant | Unknown | University of Cambridge | 12 | 2024-01-02 | 2024-07-22 | |
| Fabry Exercise Intolerance Study Intermittent cardiopulmonary exercise test, Incremental cardiopulmonary exercise test - Fabry Disease, Fabry Disease, Cardiac Variant | Unknown | Academisch Medisch Centrum - Universiteit van Amsterdam (AMC-UvA) | 30 | 2021-10-10 | 2023-08-24 | |
| Long-Term Follow-up of Subjects Who Were Treated With ST-920 ST-920 - Fabry Disease, Fabry Disease, Cardiac Variant | Active not recruiting | Sangamo Therapeutics | 32 | 2021-08-16 | 2026-08-20 | |
| Fabry Disease in High-risk Patients With Left Ventricular Hypertrophy: Prevalence and Implementation of a Clinical Score blood sampling (alpha-Galactosidase & LysoGb3) - Fabry Disease, Fabry Disease, Cardiac Variant | Not applicable | Unknown | Wuerzburg University Hospital | 200 | 2021-07-01 | 2024-06-12 |
| Natural History in Fabry Patients With IVS4+919G>A Mutation Family pedigree and data collection - Fabry Disease, Cardiac Variant | Unknown | Taipei Veterans General Hospital, Taiwan | 80 | 2017-09-01 | 2017-07-19 | |
| Myocardial Affectation in Patients With Fabry Disease Without Phenotypic Manifestation. Diagnostic Value of Biomarkers Fabry Disease, Cardiac Variant, Right Ventricular Hypertrophy | Unknown | Francisco Marín Ortuño | 120 | 2011-10-01 | 2011-09-28 | |
| Evaluation of HEArt invoLvement in Patients With FABRY Disease Rare Diseases, Fabry Disease | Recruiting | Wuerzburg University Hospital | 650 | 2001-01-01 | 2022-07-07 |
Fabry Disease (5) · Cardiomyopathy, Hypertrophic (2) · Fibrosis (2) · Rare Diseases (2) · Hypertrophy, Right Ventricular (1) · Lysosomal Storage Diseases (1) · Renal Insufficiency, Chronic (1) · Sarcoma (1) · Stroke (1)
Brain Diseases (5) · Brain Diseases, Metabolic (5) · Brain Diseases, Metabolic, Inborn (5) · Cardiovascular Diseases (5) · Central Nervous System Diseases (5) · Cerebral Small Vessel Diseases (5) · Cerebrovascular Disorders (5) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (5) · Genetic Diseases, Inborn (5) · Genetic Diseases, X-Linked (5) · Lipid Metabolism Disorders (5) · Lipid Metabolism, Inborn Errors (5) · Lipidoses (5) · Lysosomal Storage Diseases, Nervous System (5) · Metabolic Diseases (5)
Blood Specimen Collection (1) · Data Collection (1)
Wuerzburg University Hospital (2) · Academisch Medisch Centrum - Universiteit van Amsterdam (AMC-UvA) (1) · China National Center for Cardiovascular Diseases (1) · Francisco Marín Ortuño (1) · Sangamo Therapeutics (1) · Taipei Veterans General Hospital, Taiwan (1) · University of Cambridge (1)
Germany (3) · United Kingdom (2) · Australia (1) · Canada (1) · China (1) · Netherlands (1) · United States (1)
Lei Song (1) · Peter Nordbeck, MD, PhD (1)
PMID 27059467, PMID 27247331, PMID 27265676, PMID 28385306, PMID 28682471, PMID 29018006, PMID 29161295, PMID 29797054, PMID 30018776, PMID 35212486, PMID 36697134, PMID 39800432, PMID 42004908