Congenital Muscular Dystrophy: Clinical Trials

2 trials for Congenital Muscular Dystrophy, newest first

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1 completed, 1 recruiting. 2 Not applicable.

By phase and status

PhaseTrialsStatus
Not applicable2Completed 1, Recruiting 1

Follow Congenital Muscular Dystrophy: new trials by email Literature Review of Congenital Muscular Dystrophy trials Research Report on Congenital Muscular Dystrophy

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Assessments in Patients With Muscular Pathology and in Control Subjects : The ActiLiège Next Study
ActiMyo/Syde - Duchenne Muscular Dystrophy, Fascioscapulohumeral Muscular Dystrophy
Not applicableRecruitingCentre Hospitalier Universitaire de Liege3002020-07-102025-05-20
A Study to Test Lung Stretch Therapy (Hyperinsufflation) in Children With Collagen VI Muscular Dystrophy
Hyperinsufflation therapy - Congenital Muscular Dystrophy
Not applicableCompletedChildren's Hospital Medical Center, Cincinnati342013-04-012016-07-26

Narrower conditions

Charcot-Marie-Tooth Disease (1)  ·  Muscular Dystrophy, Duchenne (1)  ·  Muscular Dystrophy, Facioscapulohumeral (1)  ·  Myopathies, Structural, Congenital (1)  ·  Myotonic Dystrophy (1)

Broader conditions

Congenital Abnormalities (1)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1)  ·  Genetic Diseases, Inborn (1)  ·  Genetic Diseases, X-Linked (1)  ·  Hereditary Sensory and Motor Neuropathy (1)  ·  Heredodegenerative Disorders, Nervous System (1)  ·  Muscular Diseases (1)  ·  Muscular Disorders, Atrophic (1)  ·  Muscular Dystrophies (1)  ·  Musculoskeletal Diseases (1)  ·  Myotonic Disorders (1)  ·  Nervous System Diseases (1)  ·  Nervous System Malformations (1)  ·  Neurodegenerative Diseases (1)  ·  Neuromuscular Diseases (1)

Sponsors

Centre Hospitalier Universitaire de Liege (1)  ·  Children's Hospital Medical Center, Cincinnati (1)

Countries

Belgium (1)  ·  Czechia (1)  ·  Egypt (1)  ·  Hungary (1)  ·  Poland (1)  ·  Romania (1)  ·  Slovenia (1)  ·  United States (1)

Top investigators

Raouf S Amin, MD (1)

NIH funding

R34HL113390 (1)