1 completed, 1 recruiting. 2 Not applicable.
| Phase | Trials | Status |
|---|---|---|
| Not applicable | 2 | Completed 1, Recruiting 1 |
Follow Congenital Muscular Dystrophy: new trials by email Literature Review of Congenital Muscular Dystrophy trials Research Report on Congenital Muscular Dystrophy
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Assessments in Patients With Muscular Pathology and in Control Subjects : The ActiLiège Next Study ActiMyo/Syde - Duchenne Muscular Dystrophy, Fascioscapulohumeral Muscular Dystrophy | Not applicable | Recruiting | Centre Hospitalier Universitaire de Liege | 300 | 2020-07-10 | 2025-05-20 |
| A Study to Test Lung Stretch Therapy (Hyperinsufflation) in Children With Collagen VI Muscular Dystrophy Hyperinsufflation therapy - Congenital Muscular Dystrophy | Not applicable | Completed | Children's Hospital Medical Center, Cincinnati | 34 | 2013-04-01 | 2016-07-26 |
Charcot-Marie-Tooth Disease (1) · Muscular Dystrophy, Duchenne (1) · Muscular Dystrophy, Facioscapulohumeral (1) · Myopathies, Structural, Congenital (1) · Myotonic Dystrophy (1)
Congenital Abnormalities (1) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (1) · Genetic Diseases, Inborn (1) · Genetic Diseases, X-Linked (1) · Hereditary Sensory and Motor Neuropathy (1) · Heredodegenerative Disorders, Nervous System (1) · Muscular Diseases (1) · Muscular Disorders, Atrophic (1) · Muscular Dystrophies (1) · Musculoskeletal Diseases (1) · Myotonic Disorders (1) · Nervous System Diseases (1) · Nervous System Malformations (1) · Neurodegenerative Diseases (1) · Neuromuscular Diseases (1)
Centre Hospitalier Universitaire de Liege (1) · Children's Hospital Medical Center, Cincinnati (1)
Belgium (1) · Czechia (1) · Egypt (1) · Hungary (1) · Poland (1) · Romania (1) · Slovenia (1) · United States (1)
Raouf S Amin, MD (1)
R34HL113390 (1)