3 completed, 2 recruiting, 1 unknown. 2 Not applicable, 1 Phase 1, 1 Phase 4.
| Phase | Trials | Status |
|---|---|---|
| Not applicable | 2 | Completed 1, Recruiting 1 |
| Phase 1 | 1 | Completed 1 |
| Phase 4 | 1 | Completed 1 |
Follow Congenital Muscular Dystrophy: new trials by email Literature Review of Congenital Muscular Dystrophy trials Research Report on Congenital Muscular Dystrophy
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| Assessments in Patients With Muscular Pathology and in Control Subjects : The ActiLiège Next Study ActiMyo/Syde - Duchenne Muscular Dystrophy, Fascioscapulohumeral Muscular Dystrophy | Not applicable | Recruiting | Centre Hospitalier Universitaire de Liege | 300 | 2020-07-10 | 2025-05-20 |
| Swiss Registry for Neuromuscular Disorders SMA, DMD | Recruiting | University of Bern | 2000 | 2018-06-20 | 2026-01-15 | |
| Congenital Muscular Dystrophy Ascending Multiple Dose Cohort Study Analyzing Pharmacokinetics at Three Dose Levels In Children and Adolescents With Assessment of Safety and Tolerability of Omigapil (CALLISTO) Omigapil - Congenital Muscular Dystrophy | Phase 1 | Completed | Santhera Pharmaceuticals | 20 | 2014-12-01 | 2021-09-24 |
| Global FKRP Registry Patient Registry - LGMD2I, LGMDR9 | Unknown | Newcastle University | 1000 | 2013-11-01 | 2024-01-30 | |
| A Study to Test Lung Stretch Therapy (Hyperinsufflation) in Children With Collagen VI Muscular Dystrophy Hyperinsufflation therapy - Congenital Muscular Dystrophy | Not applicable | Completed | Children's Hospital Medical Center, Cincinnati | 34 | 2013-04-01 | 2016-07-26 |
| Flu Vaccine Study in Neuromuscular Patients 2011 2011-2012 seasonal flu vaccine Subcutaneous, 2011-2012 seasonal flu vaccine Intramuscular - Duchenne Muscular Dystrophy, Spinal Muscular Atrophy | Phase 4 | Completed | Children's Hospital Medical Center, Cincinnati | 22 | 2011-08-01 | 2020-10-19 |
Muscular Dystrophy, Duchenne (2) · Charcot-Marie-Tooth Disease (1) · Influenza, Human (1) · Muscular Atrophy, Spinal (1) · Muscular Dystrophies, Limb-Girdle (1) · Muscular Dystrophy, Facioscapulohumeral (1) · Muscular Dystrophy, Limb-Girdle, Type 2I (1) · Myopathies, Structural, Congenital (1) · Myotonic Dystrophy (1) · Walker-Warburg Syndrome (1)
Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3) · Genetic Diseases, Inborn (3) · Muscular Diseases (3) · Muscular Disorders, Atrophic (3) · Muscular Dystrophies (3) · Musculoskeletal Diseases (3) · Nervous System Diseases (3) · Neuromuscular Diseases (3) · Congenital Abnormalities (2) · Genetic Diseases, X-Linked (2) · Nervous System Malformations (2) · Neurodegenerative Diseases (2) · Central Nervous System Diseases (1) · Cobblestone Lissencephaly (1) · Eye Diseases (1)
Influenza Vaccines (1) · dibenzo(b,f)oxepin-10-ylmethyl-methyl-prop-2-ynyl-amine (1)
Children's Hospital Medical Center, Cincinnati (2) · Centre Hospitalier Universitaire de Liege (1) · Newcastle University (1) · Santhera Pharmaceuticals (1) · University of Bern (1)
United States (2) · Belgium (1) · Czechia (1) · Egypt (1) · Hungary (1) · Poland (1) · Romania (1) · Slovenia (1) · Switzerland (1) · United Kingdom (1)
Brenda Wong, MD (1) · Claudia E Kuehni, Prof. MD (1) · Raouf S Amin, MD (1) · Volker Straub, MD, PhD (1)
2018 (1), R34HL113390 (1)