Alport Syndrome, X-Linked: Clinical Trials

3 trials for Alport Syndrome, X-Linked, newest first

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1 active not recruiting, 1 completed, 1 recruiting. 2 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 22Completed 1, Recruiting 1

Follow Alport Syndrome, X-Linked: new trials by email Literature Review of Alport Syndrome, X-Linked trials Research Report on Alport Syndrome, X-Linked

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
EXACT Study: A Blinded Study in Patients With Alport Syndrome to Evaluate Exaluren Efficacy and Safety
Exaluren - Alport Syndrome, X-Linked, Alport Syndrome, Autosomal Recessive
Phase 2RecruitingEloxx Pharmaceuticals, Inc.242026-06-302026-09-30
Study of Hydroxychloroquine in Patients With X-linked Alport Syndrome in China (CHXLAS)
Hydroxychloroquine Sulfate 100 milligram (mg) Tab, Benazepril hydrochloride 10 milligram (mg) Tab - Alport Syndrome, X-Linked
Phase 2CompletedShanghai Children's Hospital502021-09-082026-03-02
Early Check: Expanded Screening in Newborns
Confirmatory Testing - Spinal Muscular Atrophy, Fragile X Syndrome
Active not recruitingRTI International300002018-10-152026-07-01

Narrower conditions

Nephritis, Hereditary (3)  ·  3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency (1)  ·  3-Hydroxyacyl-CoA Dehydrogenase Deficiency (1)  ·  3-methylcrotonyl CoA carboxylase 1 deficiency (1)  ·  3-methylcrotonyl CoA carboxylase 2 deficiency (1)  ·  Acidemia, isovaleric (1)  ·  Acrodermatitis enteropathica (1)  ·  Adenine phosphoribosyltransferase deficiency (1)  ·  Adrenal hyperplasia, congenital, type 5 (1)  ·  Adrenocorticotropic hormone deficiency (1)  ·  Amaurosis congenita of Leber, type 2 (1)  ·  Anemia, Sickle Cell (1)  ·  Angelman Syndrome (1)  ·  Aortic Stenosis, Supravalvular (1)  ·  Arginine-Glycine Amidinotransferase Deficiency (1)

Broader conditions

Collagen Diseases (3)  ·  Congenital Abnormalities (3)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (3)  ·  Connective Tissue Diseases (3)  ·  Female Urogenital Diseases (3)  ·  Female Urogenital Diseases and Pregnancy Complications (3)  ·  Kidney Diseases (3)  ·  Male Urogenital Diseases (3)  ·  Nephritis (3)  ·  Skin and Connective Tissue Diseases (3)  ·  Urogenital Abnormalities (3)  ·  Urogenital Diseases (3)  ·  Urologic Diseases (3)  ·  Abnormalities, Multiple (1)  ·  Albinism (1)

Interventions

Tablets (1)  ·  benazepril (1)

Sponsors

Eloxx Pharmaceuticals, Inc. (1)  ·  RTI International (1)  ·  Shanghai Children's Hospital (1)

Countries

United States (2)  ·  China (1)  ·  United Kingdom (1)

Top investigators

Curt Scharfe, MD, PhD (1)  ·  Wen-yan Huang, PhD (1)

Results publications

PMID 31315600, PMID 35142618