alpha-Thalassemia: Clinical Trials

2 trials for alpha-Thalassemia, newest first

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2 completed. 2 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 22Completed 2

Follow alpha-Thalassemia: new trials by email Literature Review of alpha-Thalassemia trials Research Report on alpha-Thalassemia

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Study of Etavopivat in Patients With Thalassemia or Sickle Cell Disease
Etavopivat tablets - Sickle Cell Disease, Thalassemia
Phase 2CompletedForma Therapeutics, Inc.532022-03-282025-12-16
Efficacy and Safety of Deferasirox in Non-transfusion Dependent Thalassemia Patients With Iron Overload and a One Year Open-label Extension Study
deferasirox, placebo - Non-transfusion Dependent Thalassemia
Phase 2CompletedNovartis Pharmaceuticals1662008-11-012013-07-09

Narrower conditions

Thalassemia (2)  ·  beta-Thalassemia (2)  ·  Anemia (1)  ·  Anemia, Hemolytic (1)  ·  Anemia, Sickle Cell (1)  ·  Genetic Diseases, Inborn (1)  ·  Hematologic Diseases (1)  ·  Hemoglobinopathies (1)  ·  Hemolysis (1)  ·  Iron Overload (1)  ·  Sickle Cell Trait (1)  ·  Vaso-Occlusive Crises (1)

Broader conditions

Anemia, Hemolytic, Congenital (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Hemic and Lymphatic Diseases (2)  ·  Anemia (1)  ·  Anemia, Hemolytic (1)  ·  Genetic Diseases, Inborn (1)  ·  Hematologic Diseases (1)  ·  Hemoglobinopathies (1)  ·  Iron Metabolism Disorders (1)  ·  Metabolic Diseases (1)  ·  Nutritional and Metabolic Diseases (1)  ·  Pathologic Processes (1)  ·  Pathological Conditions, Signs and Symptoms (1)

Interventions

Deferasirox (1)

Sponsors

Forma Therapeutics, Inc. (1)  ·  Novartis Pharmaceuticals (1)

Countries

Italy (2)  ·  Lebanon (2)  ·  United Kingdom (2)  ·  United States (2)  ·  Canada (1)  ·  Egypt (1)  ·  Greece (1)  ·  Malaysia (1)  ·  Taiwan (1)  ·  Thailand (1)  ·  Turkey (Türkiye) (1)

Results publications

PMID 23553596, PMID 25212456