alpha-1-Antitrypsin Deficiency, Autosomal Recessive: Clinical Trials

2 trials for alpha-1-Antitrypsin Deficiency, Autosomal Recessive, newest first

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1 enrolling by invitation, 1 no longer available. .

Follow alpha-1-Antitrypsin Deficiency, Autosomal Recessive: new trials by email Literature Review of alpha-1-Antitrypsin Deficiency, Autosomal Recessive trials Research Report on alpha-1-Antitrypsin Deficiency, Autosomal Recessive

Trials newest first · largest first

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
AATD-Liver Scan Study
Alpha-1 Antitrypsin Deficiency, AATD
Enrolling by invitationAlpha-1 Foundation10002026-01-272026-10-27
Early Access Program Using Alpha 1 Antitrypsin Infusion for Patients With Steroid Refractory Acute GvHD After Hematopoietic Stem Cell Transplantation (HSCT)
Glassia - Acute-graft-versus-host Disease, Steroid Refractory Acute Graft Versus Host Disease
No longer availableImpatients N.V. trading as myTomorrows2020-10-05

Narrower conditions

alpha 1-Antitrypsin Deficiency (2)  ·  Graft vs Host Disease (1)

Broader conditions

Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Digestive System Diseases (2)  ·  Emphysema (2)  ·  Genetic Diseases, Inborn (2)  ·  Liver Diseases (2)  ·  Lung Diseases (2)  ·  Pathologic Processes (2)  ·  Pathological Conditions, Signs and Symptoms (2)  ·  Respiratory Tract Diseases (2)  ·  Subcutaneous Emphysema (2)  ·  Immune System Diseases (1)

Interventions

alpha 1-Antitrypsin (1)

Sponsors

Alpha-1 Foundation (1)  ·  Impatients N.V. trading as myTomorrows (1)

Countries

United States (1)

Top investigators

Arpan Mohanty, MD (1)  ·  Jeanine D'Armiento, MD, PhD (1)