Adrenal Insufficiency: Clinical Trials

2 trials for Adrenal Insufficiency, newest first

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2 terminated. 2 Phase 1, 2 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 12Terminated 2
Phase 22Terminated 2

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Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
A Study to Evaluate Administration of SBT101 Gene Therapy in Adult Patients With Adrenomyeloneuropathy (AMN)
SBT101 Treatment - AMN, AMN Gene Mutation
Phase 1 / Phase 2TerminatedSwanBio Therapeutics, Inc.92022-11-172026-08-26
Phase I/II Pilot Study of Mixed Chimerism to Treat Inherited Metabolic Disorders
hematopoietic stem cell infusion - Hurler Syndrome (MPS I), Hurler-Scheie Syndrome
Phase 1 / Phase 2TerminatedTalaris Therapeutics Inc.32011-04-012023-04-12

Narrower conditions

Adrenoleukodystrophy (2)  ·  Brain Diseases, Metabolic (1)  ·  Brain Diseases, Metabolic, Inborn (1)  ·  Demyelinating Diseases (1)  ·  Hereditary Central Nervous System Demyelinating Diseases (1)  ·  Heredodegenerative Disorders, Nervous System (1)  ·  Leukodystrophy, Globoid Cell (1)  ·  Leukodystrophy, Metachromatic (1)  ·  Leukoencephalopathies (1)  ·  Metabolic Diseases (1)  ·  Metabolism, Inborn Errors (1)  ·  Mucopolysaccharidosis I (1)  ·  Mucopolysaccharidosis II (1)  ·  Mucopolysaccharidosis III (1)

Broader conditions

Adrenal Gland Diseases (2)  ·  Brain Diseases (2)  ·  Central Nervous System Diseases (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Endocrine System Diseases (2)  ·  Genetic Diseases, Inborn (2)  ·  Genetic Diseases, X-Linked (2)  ·  Intellectual Disability (2)  ·  Nervous System Diseases (2)  ·  Neurobehavioral Manifestations (2)  ·  Neurologic Manifestations (2)  ·  Nutritional and Metabolic Diseases (2)  ·  Pathological Conditions, Signs and Symptoms (2)  ·  X-Linked Intellectual Disability (2)

Interventions

Stem Cell Transplantation (1)

Sponsors

SwanBio Therapeutics, Inc. (1)  ·  Talaris Therapeutics Inc. (1)

Countries

United States (2)  ·  Netherlands (1)

Top investigators

Suzanne T Ildstad, MD (1)