2 terminated. 2 Phase 1, 2 Phase 2.
| Phase | Trials | Status |
|---|---|---|
| Phase 1 | 2 | Terminated 2 |
| Phase 2 | 2 | Terminated 2 |
Follow Adrenal Insufficiency: new trials by email Literature Review of Adrenal Insufficiency trials Research Report on Adrenal Insufficiency
Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.
| Trial | Phase | Status | Sponsor | Enrollment | Start | Updated |
|---|---|---|---|---|---|---|
| A Study to Evaluate Administration of SBT101 Gene Therapy in Adult Patients With Adrenomyeloneuropathy (AMN) SBT101 Treatment - AMN, AMN Gene Mutation | Phase 1 / Phase 2 | Terminated | SwanBio Therapeutics, Inc. | 9 | 2022-11-17 | 2026-08-26 |
| Phase I/II Pilot Study of Mixed Chimerism to Treat Inherited Metabolic Disorders hematopoietic stem cell infusion - Hurler Syndrome (MPS I), Hurler-Scheie Syndrome | Phase 1 / Phase 2 | Terminated | Talaris Therapeutics Inc. | 3 | 2011-04-01 | 2023-04-12 |
Adrenoleukodystrophy (2) · Brain Diseases, Metabolic (1) · Brain Diseases, Metabolic, Inborn (1) · Demyelinating Diseases (1) · Hereditary Central Nervous System Demyelinating Diseases (1) · Heredodegenerative Disorders, Nervous System (1) · Leukodystrophy, Globoid Cell (1) · Leukodystrophy, Metachromatic (1) · Leukoencephalopathies (1) · Metabolic Diseases (1) · Metabolism, Inborn Errors (1) · Mucopolysaccharidosis I (1) · Mucopolysaccharidosis II (1) · Mucopolysaccharidosis III (1)
Adrenal Gland Diseases (2) · Brain Diseases (2) · Central Nervous System Diseases (2) · Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2) · Endocrine System Diseases (2) · Genetic Diseases, Inborn (2) · Genetic Diseases, X-Linked (2) · Intellectual Disability (2) · Nervous System Diseases (2) · Neurobehavioral Manifestations (2) · Neurologic Manifestations (2) · Nutritional and Metabolic Diseases (2) · Pathological Conditions, Signs and Symptoms (2) · X-Linked Intellectual Disability (2)
SwanBio Therapeutics, Inc. (1) · Talaris Therapeutics Inc. (1)
United States (2) · Netherlands (1)