Tuberous Sclerosis: Clinical Trials

2 trials for Tuberous Sclerosis, newest first

ClinicalTrials Daily  ·  Areas  ·  Conditions  ·  Drugs  ·  Sponsors  ·  

2 active not recruiting. 2 Phase 1, 2 Phase 2.

By phase and status

PhaseTrialsStatus
Phase 12Active not recruiting 2
Phase 22Active not recruiting 2

Follow Tuberous Sclerosis: new trials by email Literature Review of Tuberous Sclerosis trials Research Report on Tuberous Sclerosis

Trials (filtered) newest first · largest first

All 2 trials

Tick up to 5 trials to compare them side by side (eligibility, arms, endpoints, adverse events) in a Literature Matrix.

TrialPhaseStatusSponsorEnrollmentStartUpdated
Astroscape: A Study of Radiprodil on Safety, Tolerability, Pharmacokinetics, and Effect on Seizures and Behavioral Symptoms in Patients With TSC or FCD Type II
Radiprodil - Tuberous Sclerosis Complex, Focal Cortical Dysplasia
Phase 1 / Phase 2Active not recruitingGRIN Therapeutics, Inc.302024-07-102026-04-01
Feasibility of [11C]Acetate-PET in LAM and TSC
[11C]acetate - Lymphangioleiomyomatosis, Tuberous Sclerosis Complex
Phase 1 / Phase 2Active not recruitingBrigham and Women's Hospital72021-08-302026-01-21

Narrower conditions

Focal Cortical Dysplasia (1)  ·  Lymphangioleiomyomatosis (1)

Broader conditions

Congenital Abnormalities (2)  ·  Congenital, Hereditary, and Neonatal Diseases and Abnormalities (2)  ·  Genetic Diseases, Inborn (2)  ·  Hamartoma (2)  ·  Heredodegenerative Disorders, Nervous System (2)  ·  Malformations of Cortical Development (2)  ·  Malformations of Cortical Development, Group I (2)  ·  Neoplasms (2)  ·  Neoplasms, Multiple Primary (2)  ·  Neoplastic Syndromes, Hereditary (2)  ·  Nervous System Diseases (2)  ·  Nervous System Malformations (2)  ·  Neurocutaneous Syndromes (2)  ·  Neurodegenerative Diseases (2)  ·  Hemic and Lymphatic Diseases (1)

Interventions

carbon-11 acetate (1)  ·  radiprodil (1)

Sponsors

Brigham and Women's Hospital (1)  ·  GRIN Therapeutics, Inc. (1)

Countries

Australia (1)  ·  Belgium (1)  ·  Canada (1)  ·  Italy (1)  ·  Netherlands (1)  ·  Poland (1)  ·  Spain (1)  ·  United Kingdom (1)  ·  United States (1)

Top investigators

Carmen P Priolo, MD PhD (1)

NIH funding

2023 (1)